NCT02399748Recruiting
A Long-term Study for the Outcome of Pompe Disease
Source: ClinicalTrials.gov · Last updated 18 Jul 2017 · Not updated for over 12 months - ask the site whether it is still open
Brief summary (registry, in English)
Prospectively follow patients with Pompe disease underwent enzyme replacement therapy.
- Status (registry)
- Recruiting
- Study type
- Observational
- Enrollment
- 50 (estimated)
- First submitted
- 21 Mar 2015
- Start date
- Apr 2007
- Primary completion date
- Dec 2026
- Lead sponsor
- National Taiwan University Hospital
- Diseases
- Pompe disease
- NCT number
- NCT02399748
What you commit to
- Study type: Observational
- Planned participants: 50
- From Apr 2007 to the primary completion date, Dec 2026
- 1 site in 1 country
- Visits and tests: ask the trial team, the registry does not list them
Built from the registry fields of ClinicalTrials.gov. It describes the study, not your situation.
Who cannot take part
Copied verbatim from ClinicalTrials.gov and grouped by topic. Only the trial team decides who can take part.
Other
- No
Who the study is looking for
- Confirm diagnosis with Pompe disease, is or is preparing receiving enzyme replacement therapy
Sex: All · Does not accept healthy volunteers
Sites (1)
Sites in registry order. Pick your city on the disease page to sort them by distance.
| Site | City | Country | Site status |
|---|---|---|---|
| National Taiwan University Hospital Coordinator of this site? Confirm its status | Taipei | Taiwan | Recruiting |
This page is information, not medical advice. Discuss any trial with your doctor.