NCT04012671Recruiting
A Registered Cohort Study on Duchenne Muscular Dystrophy
Source: ClinicalTrials.gov · Last updated 22 Mar 2021 · Not updated for over 12 months - ask the site whether it is still open
Brief summary (registry, in English)
Dystrophinopathy is a term of X-linked recessive genetic disease, including Duchenne Muscular Dystrophy, Becker Muscular Dystrophy, and the X-linked dilated cardiomyopathy. The aim of this study is to determine the clinical spectrum and natural progression of dystrophinopathy in a prospective multicenter natural history study, to assess the clinical, genetic of patients with dystrophinopathy to optimize clinical management.
- Status (registry)
- Recruiting
- Study type
- Observational
- Enrollment
- 2000 (estimated)
- First submitted
- 7 Jul 2019
- Start date
- 1 Jul 2019
- Primary completion date
- 31 Dec 2039
- Lead sponsor
- Ning Wang, MD., PhD.
- Diseases
- Duchenne muscular dystrophy
- NCT number
- NCT04012671
What you commit to
- Study type: Observational
- Planned participants: 2000
- From 1 Jul 2019 to the primary completion date, 31 Dec 2039
- 1 site in 1 country
- Visits and tests: ask the trial team, the registry does not list them
Built from the registry fields of ClinicalTrials.gov. It describes the study, not your situation.
Who cannot take part
Copied verbatim from ClinicalTrials.gov and grouped by topic. Only the trial team decides who can take part.
Other illness
- Presence of other clinically significant illness
Who the study is looking for
- Beyond 2 years old
- Diagnosis with Duchenne Muscular Dystrophy, and female carriers, genotypically confirmed
- Diagnosis should be supported by muscle biopsy, if no genetic confirmation.
Age in the registry: 2 years to - · Sex: All · Does not accept healthy volunteers
Sites (1)
Sites in registry order. Pick your city on the disease page to sort them by distance.
| Site | City | Country | Site status |
|---|---|---|---|
| First Affiliated Hospital of Fujian Medical University Coordinator of this site? Confirm its status | Fuzhou | China | Recruiting |
This page is information, not medical advice. Discuss any trial with your doctor.