NCT04823143Completed
Natural History Study of Patients With VCP-related Disease
Natural History of Disease Progression in Individuals With a Confirmed Diagnosis of Disease Caused by Mutation of the Valosin Containing Protein (VCP) Gene
Source: ClinicalTrials.gov · Last updated 3 Apr 2026
Brief summary (registry, in English)
A natural history study to understand the expected progression of disease in patients with confirmed mutations in the VCP gene over 1 year.
- Status (registry)
- Completed
- Study type
- Observational
- Enrollment
- 44 (actual)
- First submitted
- 26 Mar 2021
- Start date
- 18 Mar 2021
- Primary completion date
- 31 Aug 2025
- Lead sponsor
- Nationwide Children's Hospital
- NCT number
- NCT04823143
What you commit to
- Study type: Observational
- Participants enrolled: 44
- From 18 Mar 2021 to the primary completion date, 31 Aug 2025
- 1 site in 1 country
- Visits and tests: ask the trial team, the registry does not list them
Built from the registry fields of ClinicalTrials.gov. It describes the study, not your situation.
Who cannot take part
Copied verbatim from ClinicalTrials.gov and grouped by topic. Only the trial team decides who can take part.
Prior treatment
- Any concomitant illness or comorbid condition that would interfere with a patient's ability to complete study procedures safely at the discretion of the site PI.
Other
- Participation in an interventional clinical trial
Who the study is looking for
- Genetically confirmed mutation in the VCP gene
- Age ≥18 years
- Willing and able to provide informed consent and follow all study procedures
Age in the registry: 18 years to - · Sex: All · Does not accept healthy volunteers
Sites (1)
Sites in registry order. Pick your city on the disease page to sort them by distance.
| Site | City | Country | Site status |
|---|---|---|---|
| Nationwide Children's Hospital Coordinator of this site? Confirm its status | Columbus | United States | Unknown status |
This page is information, not medical advice. Discuss any trial with your doctor.