NCT05444257Active, not recruitingPhase 3
A Study Evaluating the Long-term Safety and Efficacy of VX-121 Combination Therapy
A Phase 3, Open-label Study Evaluating the Long-term Safety and Efficacy of VX-121/TEZ/D-IVA Combination Therapy in Subjects With Cystic Fibrosis
Source: ClinicalTrials.gov · Last updated 9 Oct 2026
Brief summary (registry, in English)
The purpose of this study is to evaluate the long-term safety, tolerability, and efficacy of VX-121/tezacaftor/deutivacaftor (VX-121/TEZ/D-IVA) in participants with cystic fibrosis.
- Status (registry)
- Active, not recruiting
- Phase (registry)
- Phase 3
- Study type
- Interventional
- Enrollment
- 822 (actual)
- First submitted
- 29 Jun 2022
- Start date
- 8 Nov 2022
- Primary completion date
- 30 Oct 2026
- Lead sponsor
- Vertex Pharmaceuticals Incorporated
- Diseases
- Cystic fibrosis
- NCT number
- NCT05444257
- EU CT number
- 2024-514173-22-00
- EudraCT number
- 2021-000713-17
What you commit to
- Study type: Interventional · Phase 3
- Participants enrolled: 822
- From 8 Nov 2022 to the primary completion date, 30 Oct 2026
- 193 sites in 23 countries
- Visits and tests: ask the trial team, the registry does not list them
Built from the registry fields of ClinicalTrials.gov. It describes the study, not your situation.
Who cannot take part
Copied verbatim from ClinicalTrials.gov and grouped by topic. Only the trial team decides who can take part.
Other illness
- History of drug intolerance in a parent study
Other
- Pregnant or breast-feeding females at the time of enrollment in Part A
- Other protocol defined Inclusion/Exclusion criteria may apply.
Who the study is looking for
- Part A: Completed study drug treatment in a parent study VX20-121-102 (NCT05033080) and VX20-121-103 (NCT05076149); or had study drug interruption(s) in a parent study but did not permanently discontinue study drug, and completed study visits up to the last scheduled visit of the Treatment Period in the parent study
- Part B: Completed study drug treatment in Part A; or had study drug interruption(s) in Part A, but did not permanently discontinue study drug, and completed study visits up to the last scheduled visit of the Treatment Period of Part A
Age in the registry: 12 years to - · Sex: All · Does not accept healthy volunteers
Sites (193)
Sites in registry order. Save your city in your profile to sort them by distance.
| Site | City | Country | Site status |
|---|---|---|---|
| University Hospital Graz Coordinator of this site? Confirm its status | Graz | Austria | Active, not recruiting |
| Medizinische Universitaet Innsbruck Coordinator of this site? Confirm its status | Innsbruck | Austria | Active, not recruiting |
| Gemeinnuetzige Salzburger Landeskliniken Betriebsgesellschaft mbH Coordinator of this site? Confirm its status | Salzburg | Austria | Active, not recruiting |
| Medical University of Vienna Coordinator of this site? Confirm its status | Vienna | Austria | Active, not recruiting |
| Royal Prince Alfred Hospital Coordinator of this site? Confirm its status | Camperdown | Australia | Unknown status |
| The Prince Charles Hospital Coordinator of this site? Confirm its status | Chermside | Australia | Unknown status |
| Alfred Hospital Coordinator of this site? Confirm its status | Melbourne | Australia | Unknown status |
| Institute for Respiratory Health Coordinator of this site? Confirm its status | Nedlands | Australia | Unknown status |
| Telethon Kids Institute Coordinator of this site? Confirm its status | Nedlands | Australia | Unknown status |
| The Royal Children's Hospital Coordinator of this site? Confirm its status | Parkville | Australia | Unknown status |
| Queensland Children's Hospital Coordinator of this site? Confirm its status | South Brisbane | Australia | Unknown status |
| Mater Adult Hospital Coordinator of this site? Confirm its status | South Brisbane | Australia | Unknown status |
| Westmead Hospital Coordinator of this site? Confirm its status | Westmead | Australia | Unknown status |
| Hopital Erasme Coordinator of this site? Confirm its status | Anderlecht | Belgium | Active, not recruiting |
| Universitair Ziekenhuis Gent Coordinator of this site? Confirm its status | Gent | Belgium | Active, not recruiting |
| UZ Brussel Coordinator of this site? Confirm its status | Jette | Belgium | Active, not recruiting |
| UZ Leuven Coordinator of this site? Confirm its status | Leuven | Belgium | Active, not recruiting |
| Cliniques Universitaires Saint-Luc Coordinator of this site? Confirm its status | Sint-Lambrechts-Woluwe | Belgium | Active, not recruiting |
| University of Calgary Medical Clinic of the Foothills Medical Centre Coordinator of this site? Confirm its status | Calgary | Canada | Unknown status |
| Stollery Children'S Hospital Coordinator of this site? Confirm its status | Edmonton | Canada | Unknown status |
| St. Joseph's Health Care London Coordinator of this site? Confirm its status | London | Canada | Unknown status |
| McGill University Health Centre, Glen Site, Montreal Children's Hospital Coordinator of this site? Confirm its status | Montreal | Canada | Unknown status |
| Centre Hospitalier de l'Universite de Montreal (CHUM) Hotel-Dieu Coordinator of this site? Confirm its status | Montreal | Canada | Unknown status |
| Institut Universitaire de Cardiologie et Pneumologie de Quebec - Universite Laval Coordinator of this site? Confirm its status | Québec | Canada | Unknown status |
| British Columbia Children's Hospital Coordinator of this site? Confirm its status | Vancouver | Canada | Unknown status |
| St. Paul's Hospital Coordinator of this site? Confirm its status | Vancouver | Canada | Unknown status |
| Kinderspital Zuerich Coordinator of this site? Confirm its status | Zurich | Switzerland | Unknown status |
| Fakultni nemocnice Brno Coordinator of this site? Confirm its status | Brno | Czechia | Active, not recruiting |
| Fakultni nemocnice v Motole Coordinator of this site? Confirm its status | Prague | Czechia | Active, not recruiting |
| Charite Universitaetsmedizin Berlin KöR Coordinator of this site? Confirm its status | Berlin | Germany | Active, not recruiting |
| Universitaetsklinikum Erlangen AöR Coordinator of this site? Confirm its status | Erlangen | Germany | Active, not recruiting |
| Ruhrlandklinik Westdeutsches Lungenzentrum Am Universitaetsklinikum Essen gGmbH Coordinator of this site? Confirm its status | Essen | Germany | Active, not recruiting |
| Universitaetsklinikum Essen (AoR) Coordinator of this site? Confirm its status | Essen | Germany | Active, not recruiting |
| Universitaetsklinikum Frankfurt AöR Coordinator of this site? Confirm its status | Frankfurt Am Main | Germany | Active, not recruiting |
| Universitaetsklinikum Giessen und Marburg GmbH Coordinator of this site? Confirm its status | Giessen | Germany | Active, not recruiting |
| Medizinische Hochschule Hannover Coordinator of this site? Confirm its status | Hanover | Germany | Active, not recruiting |
| Universitaetsklinikum Jena KöR Coordinator of this site? Confirm its status | Jena | Germany | Active, not recruiting |
| Universitaetsmedizin der Johannes Gutenberg-Universitaet Mainz KöR Coordinator of this site? Confirm its status | Mainz | Germany | Active, not recruiting |
| Pneumological Study Center Munich-West Coordinator of this site? Confirm its status | Munich | Germany | Active, not recruiting |
| Klinikum Ernst von Bergmann gGmbH Coordinator of this site? Confirm its status | Potsdam | Germany | Active, not recruiting |
| Universitaetsklinikum Ulm AoR Coordinator of this site? Confirm its status | Ulm | Germany | Active, not recruiting |
| Universitaetsklinikum Wuerzburg AöR Coordinator of this site? Confirm its status | Wuerzburg | Germany | Active, not recruiting |
| Aarhus Universitetshospital Coordinator of this site? Confirm its status | Aarhus N | Denmark | Active, not recruiting |
| Rigshospitalet Coordinator of this site? Confirm its status | Copenhagen Oe | Denmark | Active, not recruiting |
| Hospital Universitari Vall d'Hebron Coordinator of this site? Confirm its status | Barcelona | Spain | Active, not recruiting |
| Sant Joan De Deu Barcelona Hospital Coordinator of this site? Confirm its status | Esplugues De Llobregat | Spain | Active, not recruiting |
| Hospital Universitario Ramón y Cajal Coordinator of this site? Confirm its status | Madrid | Spain | Active, not recruiting |
| Hospital Universitario 12 de Octubre Coordinator of this site? Confirm its status | Madrid | Spain | Active, not recruiting |
| University Clinical Hospital Virgen De La Arrixaca Coordinator of this site? Confirm its status | Murcia | Spain | Active, not recruiting |
| Parc Tauli Hospital Universitari Coordinator of this site? Confirm its status | Sabadell | Spain | Active, not recruiting |
| University Hospital Virgen Del Rocio S.L. Coordinator of this site? Confirm its status | Sevilla | Spain | Active, not recruiting |
| Hospital Universitario Y Politecnico La Fe Coordinator of this site? Confirm its status | Valencia | Spain | Active, not recruiting |
| Centre hospitalier Universitaire de Bordeaux Coordinator of this site? Confirm its status | Bordeaux | France | Active, not recruiting |
| Hospices Civils de Lyon Coordinator of this site? Confirm its status | Bron | France | Active, not recruiting |
| Centre Hospitalier Intercommunal Créteil Coordinator of this site? Confirm its status | Créteil | France | Active, not recruiting |
| Hopital Cardiologique Coordinator of this site? Confirm its status | Lille Cedex | France | Active, not recruiting |
| Centre Hospitalier Universitaire de Montpellier Coordinator of this site? Confirm its status | Montpellier | France | Active, not recruiting |
| Centre Hospitalier Universitaire de Nice Coordinator of this site? Confirm its status | Nice | France | Active, not recruiting |
| Assistance Publique Hopitaux de Paris Coordinator of this site? Confirm its status | Paris | France | Active, not recruiting |
| Robert Debre University Hospital Coordinator of this site? Confirm its status | Paris | France | Active, not recruiting |
| Hospices Civils de Lyon Coordinator of this site? Confirm its status | Pierre-Bénite | France | Active, not recruiting |
| Fondation ILDYS Coordinator of this site? Confirm its status | Roscoff | France | Active, not recruiting |
| Centre Hospitalier Universitaire Rouen Coordinator of this site? Confirm its status | Rouen Cedex | France | Active, not recruiting |
| Les Hopitaux Universitaires De Strasbourg Coordinator of this site? Confirm its status | Strasbourg Cedex 2 | France | Active, not recruiting |
| Hospital Foch Coordinator of this site? Confirm its status | Suresnes | France | Active, not recruiting |
| Centre Hospitalier Régional Universitaire de Tours Coordinator of this site? Confirm its status | Tours | France | Active, not recruiting |
| Birmingham Heartlands Hospital Coordinator of this site? Confirm its status | Birmingham | United Kingdom | Unknown status |
| University Hospitals Bristol and Weston NHS Foundation Trust, Bristol Royal Hospital Coordinator of this site? Confirm its status | Bristol | United Kingdom | Unknown status |
| Royal Papworth Hospital NHS Foundation Trust Coordinator of this site? Confirm its status | Cambridge | United Kingdom | Unknown status |
| Western General Hospital Coordinator of this site? Confirm its status | Edinburgh | United Kingdom | Unknown status |
| Royal Devon University Healthcare NHS Foundation Trust Coordinator of this site? Confirm its status | Exeter | United Kingdom | Unknown status |
| Clinical Research Facility, Queen Elizabeth University Hospital Coordinator of this site? Confirm its status | Glasgow | United Kingdom | Unknown status |
| St James University Hospital Coordinator of this site? Confirm its status | Leeds | United Kingdom | Unknown status |
| Leeds General Infirmary Coordinator of this site? Confirm its status | Leeds | United Kingdom | Unknown status |
| Liverpool Heart and Chest Hospital Coordinator of this site? Confirm its status | Liverpool | United Kingdom | Unknown status |
| King's College Hospital Coordinator of this site? Confirm its status | London | United Kingdom | Unknown status |
| St. Bartholomew's Hospital Coordinator of this site? Confirm its status | London | United Kingdom | Unknown status |
| Royal Brompton Hospital Coordinator of this site? Confirm its status | London | United Kingdom | Unknown status |
| Royal Manchester Children's Hospital Coordinator of this site? Confirm its status | Manchester | United Kingdom | Unknown status |
| Wythenshawe Hospital Coordinator of this site? Confirm its status | Manchester | United Kingdom | Unknown status |
| Clinical Research Facility Coordinator of this site? Confirm its status | Newcastle upon Tyne | United Kingdom | Unknown status |
| All Wales Adult Cystic Fibrosis Centre, University Hospital Llandough Coordinator of this site? Confirm its status | Penarth | United Kingdom | Unknown status |
| Southampton General Hospital Coordinator of this site? Confirm its status | Southampton | United Kingdom | Unknown status |
| Geniko Nosokomeio Thessalonikis George Papanikolaou Coordinator of this site? Confirm its status | Thessaloniki | Greece | Active, not recruiting |
| Ippokratio General Hospital of Thessaloniki Coordinator of this site? Confirm its status | Thessaloniki | Greece | Active, not recruiting |
| Orszagos Koranyi Pulmonologiai Intezet Coordinator of this site? Confirm its status | Budapest XII | Hungary | Active, not recruiting |
| Református Pulmonológiai Centrum Coordinator of this site? Confirm its status | Törökbálint | Hungary | Active, not recruiting |
| Cork University Hospital Coordinator of this site? Confirm its status | Cork | Ireland | Active, not recruiting |
| Children's Health Ireland Coordinator of this site? Confirm its status | Dublin 1 | Ireland | Active, not recruiting |
| Children's Health Ireland Coordinator of this site? Confirm its status | Dublin 12 | Ireland | Active, not recruiting |
| St Vincent's University Hospital Coordinator of this site? Confirm its status | Dublin 4 | Ireland | Active, not recruiting |
| University Hospital Limerick Coordinator of this site? Confirm its status | Limerick | Ireland | Active, not recruiting |
| Hadassah Medical Organization Coordinator of this site? Confirm its status | Jerusalem | Israel | Unknown status |
| Clalit Health Services Coordinator of this site? Confirm its status | Petach Tikvah | Israel | Unknown status |
| Safra Children's Hospital Coordinator of this site? Confirm its status | Tel HaShomer | Israel | Unknown status |
| Azienda Ospedaliero-Universitaria delle Marche Coordinator of this site? Confirm its status | Ancona | Italy | Active, not recruiting |
| Azienda Ospedaliera Universitaria Meyer IRCCS Coordinator of this site? Confirm its status | Florence | Italy | Active, not recruiting |
| IRCCS Istituto Giannina Gaslini Coordinator of this site? Confirm its status | Genoa | Italy | Active, not recruiting |
| Fondazione IRCCS Cà Granda Ospedale Maggiore Policlinico Coordinator of this site? Confirm its status | Milan | Italy | Active, not recruiting |
| Azienda Ospedaliero-Universitaria San Luigi Gonzaga Coordinator of this site? Confirm its status | Orbassano | Italy | Active, not recruiting |
| Azienda Ospedaliera Regionale San Carlo Coordinator of this site? Confirm its status | Potenza | Italy | Active, not recruiting |
| Azienda Ospedaliera Universitaria Integrata Verona Coordinator of this site? Confirm its status | Verona | Italy | Active, not recruiting |
| Stichting Amsterdam UMC Coordinator of this site? Confirm its status | Amsterdam | Netherlands | Active, not recruiting |
| Radboud Universitair Medisch Centrum (Radboudumc) Coordinator of this site? Confirm its status | Nijmegen | Netherlands | Active, not recruiting |
| Erasmus Universitair Medisch Centrum Rotterdam (Erasmus MC) Coordinator of this site? Confirm its status | Rotterdam | Netherlands | Active, not recruiting |
| Haga Hospital Coordinator of this site? Confirm its status | 's-Gravenhage | Netherlands | Active, not recruiting |
| Universitair Medisch Centrum Utrecht Coordinator of this site? Confirm its status | Utrecht | Netherlands | Active, not recruiting |
| Helse Bergen HF Coordinator of this site? Confirm its status | Bergen | Norway | Active, not recruiting |
| Oslo University Hospital HF Coordinator of this site? Confirm its status | Oslo | Norway | Active, not recruiting |
| Canterbury District Health Board Coordinator of this site? Confirm its status | Christchurch | New Zealand | Unknown status |
| Starship Children's Hospital Coordinator of this site? Confirm its status | Grafton | New Zealand | Unknown status |
| Waikato Hospital Coordinator of this site? Confirm its status | Hamilton | New Zealand | Unknown status |
| Greenlane Clinical Centre Coordinator of this site? Confirm its status | One Tree Hill | New Zealand | Unknown status |
| Szpital Dzieciecy Polanki Im. Macieja Plazynskiego W Gdansku Sp. z o.o. Coordinator of this site? Confirm its status | Gdansk | Poland | Active, not recruiting |
| Samodzielny Zespol Publicznych Zakladow Opieki Zdrowotnej Im. Dzieci Warszawy W Dziekanowie Lesnym Coordinator of this site? Confirm its status | Lomianki | Poland | Active, not recruiting |
| Unidade Local De Saude De Santa Maria E.P.E. Coordinator of this site? Confirm its status | Lisbon | Portugal | Active, not recruiting |
| Unidade Local De Saude De Santo Antonio E.P.E. Coordinator of this site? Confirm its status | Porto | Portugal | Active, not recruiting |
| Unidade Local de Saude de Sao Joao E.P.E. Coordinator of this site? Confirm its status | Porto | Portugal | Active, not recruiting |
| Sahlgrenska University Hospital-Vaestra Goetalandsregionen Coordinator of this site? Confirm its status | Goteborg | Sweden | Active, not recruiting |
| Karolinska University Hospital Coordinator of this site? Confirm its status | Huddinge | Sweden | Active, not recruiting |
| Region Skane Skanes Universitetssjukhus Coordinator of this site? Confirm its status | Lund | Sweden | Active, not recruiting |
| Akron Children's Hospital Coordinator of this site? Confirm its status | Akron | United States | Unknown status |
| Albany Medical College, Pulmonary and Critical Care Medicine Coordinator of this site? Confirm its status | Albany | United States | Unknown status |
| Michigan Medicine Coordinator of this site? Confirm its status | Ann Arbor | United States | Unknown status |
| The Emory Clinic at Chantilly Coordinator of this site? Confirm its status | Atlanta | United States | Unknown status |
| Augusta University Coordinator of this site? Confirm its status | Augusta | United States | Unknown status |
| Children's Hospital of Colorado Coordinator of this site? Confirm its status | Aurora | United States | Unknown status |
| Billings Clinic Coordinator of this site? Confirm its status | Billings | United States | Unknown status |
| University of Alabama at Birmingham Coordinator of this site? Confirm its status | Birmingham | United States | Unknown status |
| St. Luke's Cystic Fibrosis Center of Idaho Coordinator of this site? Confirm its status | Boise | United States | Unknown status |
| Massachusetts General Hospital Cystic Fibrosis Center Clinical Research Center Coordinator of this site? Confirm its status | Boston | United States | Unknown status |
| Boston Children's Hospital Coordinator of this site? Confirm its status | Boston | United States | Unknown status |
| CF Therapeutics Development Center of Western New York Coordinator of this site? Confirm its status | Buffalo | United States | Unknown status |
| Atrium Health/Levine Children's Hospital Coordinator of this site? Confirm its status | Charlotte | United States | Unknown status |
| University of Virginia Health System Coordinator of this site? Confirm its status | Charlottesville | United States | Unknown status |
| Northwestern Memorial Hospital Coordinator of this site? Confirm its status | Chicago | United States | Unknown status |
| Vermont Lung Center Coordinator of this site? Confirm its status | Colchester | United States | Unknown status |
| Prisma Health Richland Campus Coordinator of this site? Confirm its status | Columbia | United States | Unknown status |
| Childrens Hospital University of Missouri Health Sciences Center Coordinator of this site? Confirm its status | Columbia | United States | Unknown status |
| Nationwide Children's Hospital Coordinator of this site? Confirm its status | Columbus | United States | Unknown status |
| The University of Texas Southwestern Medical Center Coordinator of this site? Confirm its status | Dallas | United States | Unknown status |
| Dayton Children's Hospital Coordinator of this site? Confirm its status | Dayton | United States | Unknown status |
| National Jewish Health Coordinator of this site? Confirm its status | Denver | United States | Unknown status |
| Harper University Hospital Coordinator of this site? Confirm its status | Detroit | United States | Unknown status |
| Cook Children's Health Care System Coordinator of this site? Confirm its status | Fort Worth | United States | Unknown status |
| University of Florida Shands Hospital Coordinator of this site? Confirm its status | Gainesville | United States | Unknown status |
| Spectrum Health Medical Group Adult Cystic Fibrosis Care Center Coordinator of this site? Confirm its status | Grand Rapids | United States | Unknown status |
| New York Medical College Coordinator of this site? Confirm its status | Hawthorne | United States | Unknown status |
| Joe DiMaggio Cystic Fibrosis & Pulmonary Center Coordinator of this site? Confirm its status | Hollywood | United States | Unknown status |
| Texas Children's Hospital/ Baylor College of Medicine Coordinator of this site? Confirm its status | Houston | United States | Unknown status |
| Indiana University Coordinator of this site? Confirm its status | Indianapolis | United States | Unknown status |
| Riley Hospital for Children at Indiana University Health Coordinator of this site? Confirm its status | Indianapolis | United States | Unknown status |
| The Children's Mercy Hospital Coordinator of this site? Confirm its status | Kansas City | United States | Unknown status |
| University of Kansas Medical Center Coordinator of this site? Confirm its status | Kansas City | United States | Unknown status |
| University of Tennessee Medical Center Coordinator of this site? Confirm its status | Knoxville | United States | Unknown status |
| University of Kentucky Coordinator of this site? Confirm its status | Lexington | United States | Unknown status |
| University of Arkansas for Medical Sciences Coordinator of this site? Confirm its status | Little Rock | United States | Unknown status |
| Miller Children's Hospital / Long Beach Memorial Coordinator of this site? Confirm its status | Long Beach | United States | Unknown status |
| Children's Hospital Los Angeles Coordinator of this site? Confirm its status | Los Angeles | United States | Unknown status |
| University Hospital and UW Health Clinics Coordinator of this site? Confirm its status | Madison | United States | Unknown status |
| Dartmouth Hitchcock Coordinator of this site? Confirm its status | Manchester | United States | Unknown status |
| University of Miami Miller School of Medicine Coordinator of this site? Confirm its status | Miami | United States | Unknown status |
| University of Minnesota Coordinator of this site? Confirm its status | Minneapolis | United States | Unknown status |
| West Virginia University Coordinator of this site? Confirm its status | Morgantown | United States | Unknown status |
| Morristown Medical Center Coordinator of this site? Confirm its status | Morristown | United States | Unknown status |
| Vanderbilt University Medical Center - Nephrology Clinical Trials Center Coordinator of this site? Confirm its status | Nashville | United States | Unknown status |
| Long Island Jewish Medical Center Coordinator of this site? Confirm its status | New Hyde Park | United States | Unknown status |
| Tulane Medical Center Coordinator of this site? Confirm its status | New Orleans | United States | Unknown status |
| Columbia University Medical Center Coordinator of this site? Confirm its status | New York | United States | Unknown status |
| Kaiser Permanente Coordinator of this site? Confirm its status | Oakland | United States | Unknown status |
| Santiago Reyes, M.D. Coordinator of this site? Confirm its status | Oklahoma City | United States | Unknown status |
| University of Oklahoma Health Sciences Center Coordinator of this site? Confirm its status | Oklahoma City | United States | Unknown status |
| Nebraska Medical Center Coordinator of this site? Confirm its status | Omaha | United States | Unknown status |
| Central Florida Pulmonary Group, PA Coordinator of this site? Confirm its status | Orlando | United States | Unknown status |
| Nemours Children's Specialty Care Coordinator of this site? Confirm its status | Pensacola | United States | Unknown status |
| Children's Hospital of Philadelphia Coordinator of this site? Confirm its status | Philadelphia | United States | Unknown status |
| UPMC Children's Hospital of Pittsburgh Coordinator of this site? Confirm its status | Pittsburgh | United States | Unknown status |
| Oregon Health Science University Coordinator of this site? Confirm its status | Portland | United States | Unknown status |
| Maine Medical Partners Coordinator of this site? Confirm its status | Portland | United States | Unknown status |
| University of California, Davis Medical Center Coordinator of this site? Confirm its status | Sacramento | United States | Unknown status |
| University of Utah Coordinator of this site? Confirm its status | Salt Lake City | United States | Unknown status |
| University of California San Francisco, Lung Transplant Program Coordinator of this site? Confirm its status | San Francisco | United States | Unknown status |
| University of Washington Medical Center Coordinator of this site? Confirm its status | Seattle | United States | Unknown status |
| Sanford Children's Speciality Clinic Coordinator of this site? Confirm its status | Sioux Falls | United States | Unknown status |
| Providence Pediatric Pulmonary & Cystic Fibrosis Clinic Coordinator of this site? Confirm its status | Spokane | United States | Unknown status |
| Cardinal Glennon Children's Hospital - St. Louis University Coordinator of this site? Confirm its status | St Louis | United States | Unknown status |
| Washington University School of Medicine/St. Louis Children's Hospital Coordinator of this site? Confirm its status | St Louis | United States | Unknown status |
| Johns Hopkins All Children's Hospital Outpatient Care Center Coordinator of this site? Confirm its status | St. Petersburg | United States | Unknown status |
| SUNY Upstate Medical University Coordinator of this site? Confirm its status | Syracuse | United States | Unknown status |
| ProMedica Toledo Hospital/Toledo Children's Hospital/Pediatric Pulmonary & Cystic Fibrosis Center Coordinator of this site? Confirm its status | Toledo | United States | Unknown status |
| Banner University of Arizona Medical Center Coordinator of this site? Confirm its status | Tucson | United States | Unknown status |
| Wake Forest Baptist Health Coordinator of this site? Confirm its status | Winston-Salem | United States | Unknown status |
| Umass Memorial Medical Center Coordinator of this site? Confirm its status | Worcester | United States | Unknown status |
This page is information, not medical advice. Discuss any trial with your doctor.