NCT05755451Recruiting
Natural History of SMA
Natural History of SMA: Long Term Longitudinal Study and Development of a Registry
Source: ClinicalTrials.gov · Last updated 6 Mar 2023 · Not updated for over 12 months - ask the site whether it is still open
Brief summary (registry, in English)
This is an investigator initiated observational study with the aim to record several aspects of function, care and adverse events in a large cohort of SMA patients followed longitudinally by using a structured academic disease registry.
- Status (registry)
- Recruiting
- Study type
- Observational
- Enrollment
- 1200 (estimated)
- First submitted
- 8 Feb 2023
- Start date
- 21 Jun 2018
- Primary completion date
- 30 Dec 2033
- Lead sponsor
- Fondazione Policlinico Universitario Agostino Gemelli IRCCS
- Diseases
- Spinal muscular atrophy
- NCT number
- NCT05755451
What you commit to
- Study type: Observational
- Planned participants: 1200
- From 21 Jun 2018 to the primary completion date, 30 Dec 2033
- 5 sites in 1 country
- Visits and tests: ask the trial team, the registry does not list them
Built from the registry fields of ClinicalTrials.gov. It describes the study, not your situation.
Who cannot take part
Copied verbatim from ClinicalTrials.gov and grouped by topic. Only the trial team decides who can take part.
Other
- if enrolled in clinical trials
Who the study is looking for
- all patients
Sex: All · Does not accept healthy volunteers
Sites (5)
Sites in registry order. Pick your city on the disease page to sort them by distance.
| Site | City | Country | Site status |
|---|---|---|---|
| Istituto Gaslini Coordinator of this site? Confirm its status | Genova | Italy | Recruiting |
| Nemo Sud Coordinator of this site? Confirm its status | Messina | Italy | Recruiting |
| Centro Clinico Nemo Coordinator of this site? Confirm its status | Milan | Italy | Recruiting |
| Policlinico Gemelli Coordinator of this site? Confirm its status | Rome | Italy | Recruiting |
| Ospedale Bambino gesu Coordinator of this site? Confirm its status | Rome | Italy | Recruiting |
This page is information, not medical advice. Discuss any trial with your doctor.