NCT06016946Recruiting
Friedreich Ataxia Global Clinical Consortium UNIFIED Natural History Study
Source: ClinicalTrials.gov · Last updated 1 Sept 2026
Brief summary (registry, in English)
This project is a global, multicenter, prospective, longitudinal, observational natural history study that can be used to understand the disease progression and support the development of safe and effective drugs and biological products for Friedreich ataxia.
- Status (registry)
- Recruiting
- Study type
- Observational
- Enrollment
- 3000 (estimated)
- First submitted
- 18 Aug 2023
- Start date
- 28 Jun 2023
- Primary completion date
- 28 Jan 2048
- Lead sponsor
- Friedreich's Ataxia Research Alliance
- Diseases
- Friedreich ataxia
- NCT number
- NCT06016946
What you commit to
- Study type: Observational
- Planned participants: 3000
- From 28 Jun 2023 to the primary completion date, 28 Jan 2048
- 34 sites in 17 countries
- Visits and tests: ask the trial team, the registry does not list them
Built from the registry fields of ClinicalTrials.gov. It describes the study, not your situation.
Who cannot take part
Copied verbatim from ClinicalTrials.gov and grouped by topic. Only the trial team decides who can take part.
Other illness
- Acute or ongoing medical or other conditions that would interfere with the conduct and assessments of the study
Other
- Unable or unwilling to provide informed consent
- For any reason in the opinion of the investigator, participant would be unlikely or unable to comply with study protocol requirements.
Who the study is looking for
- Both males and females of any age
- Individuals with Friedreich ataxia (FA): Participants that meet genetically confirmed diagnosis of Friedreich ataxia
- Written informed consent provided
- Informed consent must be obtained for all participants
- For underage participants, they and the parent/ legally authorized representative have to sign the informed consent form, child assent (if applicable)
- Persons who are not legally competent require the informed consent of their legally authorized representative
Sex: All · Accepts healthy volunteers
Sites (34)
Sites in registry order. Pick your city on the disease page to sort them by distance.
| Site | City | Country | Site status |
|---|---|---|---|
| Medical University Innsbruck, Department of Neurology Coordinator of this site? Confirm its status | Innsbruck | Austria | Recruiting |
| Murdoch Childrens Research Institute Coordinator of this site? Confirm its status | Parkville | Australia | Recruiting |
| Université Libre de Bruxelles, Hôpital Erasme, Dpt of Neurology Coordinator of this site? Confirm its status | Brussels | Belgium | Recruiting |
| University of Campinas Coordinator of this site? Confirm its status | Campinas | Brazil | Not yet recruiting |
| McGill University Health Centre - Montreal Neurological Institute Coordinator of this site? Confirm its status | Montreal | Canada | Recruiting |
| CHUM - Hopital Notre-Dame Coordinator of this site? Confirm its status | Montreal | Canada | Recruiting |
| The Hospital for Sick Children Coordinator of this site? Confirm its status | Toronto | Canada | Recruiting |
| Motol University Hospital, Centre for Hereditary Ataxias Coordinator of this site? Confirm its status | Prague | Czechia | Recruiting |
| University Hospital Aachen, Dept. of Neurology Coordinator of this site? Confirm its status | Aachen | Germany | Recruiting |
| Deutsches Zentrum Für Neurodegenerative Erkrankungen Coordinator of this site? Confirm its status | Bonn | Germany | Not yet recruiting |
| University of Munich, Dept. of Neurology, Friedrich-Baur-Institut Coordinator of this site? Confirm its status | Munich | Germany | Recruiting |
| University of Tübingen, Dept. of Neurodegenerative Diseases, Hertie-Institute for Clinical Brain Research Coordinator of this site? Confirm its status | Tübingen | Germany | Recruiting |
| Hospital Sant Joan de Déu, Servicio de Neurología Coordinator of this site? Confirm its status | Barcelona | Spain | Not yet recruiting |
| Hospital Universitario La Paz, Servicio de Neurologia Coordinator of this site? Confirm its status | Madrid | Spain | Not yet recruiting |
| Paris Brain Institute Coordinator of this site? Confirm its status | Paris | France | Recruiting |
| Hôpital de Hautepierre, Service de Neurologie Coordinator of this site? Confirm its status | Strasbourg | France | Not yet recruiting |
| University College of London, Ataxia Centre, National Hospital for Neurology and Neurosurgery Coordinator of this site? Confirm its status | London | United Kingdom | Not yet recruiting |
| National and Kapodistrian University of Athens, Neurogenetics Unit Coordinator of this site? Confirm its status | Athens | Greece | Recruiting |
| Tallaght University Hospital, Department of Neurology Coordinator of this site? Confirm its status | Dublin | Ireland | Recruiting |
| All India Institute of Medical Sciences(AIIMS) Coordinator of this site? Confirm its status | New Delhi | India | Recruiting |
| Referente Clinico-Scientifico di Polo IRCCS "E. Medea" Coordinator of this site? Confirm its status | Conegliano | Italy | Recruiting |
| Fondazione IRCCS Istituto Neurologico Carlo Besta Coordinator of this site? Confirm its status | Milan | Italy | Recruiting |
| Bambino Gesù Children's Hospital, Department of Neurosciences Coordinator of this site? Confirm its status | Roma | Italy | Not yet recruiting |
| Stichting Radboud Universitair Medisch Centrum Coordinator of this site? Confirm its status | Nijmegen | Netherlands | Recruiting |
| Auckland City Hospital Coordinator of this site? Confirm its status | Auckland | New Zealand | Recruiting |
| Emory University Hospital - Neurology Coordinator of this site? Confirm its status | Atlanta | United States | Recruiting |
| Ohio State University - Neurology Coordinator of this site? Confirm its status | Columbus | United States | Recruiting |
| University of Colorado Coordinator of this site? Confirm its status | Denver | United States | Recruiting |
| University of Florida - Neurology Coordinator of this site? Confirm its status | Gainesville | United States | Recruiting |
| University of Iowa Stead Family Children's Hospital Coordinator of this site? Confirm its status | Iowa City | United States | Recruiting |
| UCLA Ataxia Center Coordinator of this site? Confirm its status | Los Angeles | United States | Recruiting |
| St. Jude Children's Research Hospital Coordinator of this site? Confirm its status | Memphis | United States | Recruiting |
| Children's Hospital of Philadelphia Coordinator of this site? Confirm its status | Philadelphia | United States | Recruiting |
| USF Ataxia Research Center Coordinator of this site? Confirm its status | Tampa | United States | Recruiting |
This page is information, not medical advice. Discuss any trial with your doctor.