NCT06155500Active, not recruitingPhase 1
Long-term Follow-up (LTFU) of Patients Treated With Genome-edited Autologous Hematopoietic Stem and Progenitor Cells (HSPC)
Source: ClinicalTrials.gov · Last updated 28 Jul 2026
Brief summary (registry, in English)
CADPT03A12001 is a prospective, multi-center study that is designed to follow all enrolled patients who have received treatment with OTQ923 for long-term safety and efficacy.
- Status (registry)
- Active, not recruiting
- Phase (registry)
- Phase 1
- Study type
- Interventional
- Enrollment
- 4 (actual)
- First submitted
- 24 Nov 2023
- Start date
- 16 Apr 2024
- Primary completion date
- 11 Jan 2039
- Lead sponsor
- Novartis Pharmaceuticals
- Diseases
- Sickle cell disease
- NCT number
- NCT06155500
What you commit to
- Study type: Interventional · Phase 1
- Participants enrolled: 4
- From 16 Apr 2024 to the primary completion date, 11 Jan 2039
- 3 sites in 1 country
- Visits and tests: ask the trial team, the registry does not list them
Built from the registry fields of ClinicalTrials.gov. It describes the study, not your situation.
Who cannot take part
Copied verbatim from ClinicalTrials.gov and grouped by topic. Only the trial team decides who can take part.
Other
- 1\. Completion of less than 1 year of safety follow-up in the treatment protocol (CADPT03A12101).
Who the study is looking for
- Patients must have received gene therapy treatment from the parent treatment protocol (CADPT03A12101).
- Patients must provide informed consent prior to their entry into this study.
Age in the registry: 18 years to 100 years · Sex: All · Does not accept healthy volunteers
Sites (3)
Sites in registry order. Pick your city on the disease page to sort them by distance.
| Site | City | Country | Site status |
|---|---|---|---|
| University of Chicago Coordinator of this site? Confirm its status | Chicago | United States | Unknown status |
| St Jude Childrens Research Hospital Coordinator of this site? Confirm its status | Memphis | United States | Unknown status |
| Memorial Sloan Kettering Cancer Ctr Coordinator of this site? Confirm its status | New York | United States | Unknown status |
This page is information, not medical advice. Discuss any trial with your doctor.