NCT06488261Active, not recruiting
Long Term Follow-Up for Safety of AVR-RD-02
A Long-Term Follow-Up Safety Study of Subjects With Gaucher Disease Who Previously Received AVR-RD-02
Source: ClinicalTrials.gov · Last updated 22 Jul 2025
Brief summary (registry, in English)
The goal of this observational study is to assess the safety and tolerability of AVR-RD-02 treatment in subjects who previously received AVR-RD-02 treatment (single dose administration).
- Status (registry)
- Active, not recruiting
- Study type
- Observational
- Enrollment
- 2 (actual)
- First submitted
- 20 Nov 2023
- Start date
- 21 Feb 2024
- Primary completion date
- Jun 2037
- Lead sponsor
- John Bernat
- Diseases
- Gaucher disease
- NCT number
- NCT06488261
What you commit to
- Study type: Observational
- Participants enrolled: 2
- From 21 Feb 2024 to the primary completion date, Jun 2037
- 1 site in 1 country
- Visits and tests: ask the trial team, the registry does not list them
Built from the registry fields of ClinicalTrials.gov. It describes the study, not your situation.
Who cannot take part
Copied verbatim from ClinicalTrials.gov and grouped by topic. Only the trial team decides who can take part.
Other illness
- Subject has any medical, psychological, or other condition that, in the opinion of the Investigator:
Other
- Might interfere with the subject's participation in the study (including consenting to procedures); and/or
- Poses any additional risk to the subject; and/or
- Might confound the results of any study-required assessments.
Who the study is looking for
- Subjects must meet all of the following inclusion criteria for participation in this study:
- Subject must be willing and able to provide written informed consent for the JAB-GD-001 study in accordance with applicable regulations and guidelines and to comply with all study visits and procedures.
- Subject must have been enrolled in the preceding AVROBIO AVRO-RD-02-201 treatment study and have received AVR-RD-02 treatment
Age in the registry: 18 years to - · Sex: All · Does not accept healthy volunteers
Sites (1)
Sites in registry order. Pick your city on the disease page to sort them by distance.
| Site | City | Country | Site status |
|---|---|---|---|
| University of Iowa Hospitals and Clinics Coordinator of this site? Confirm its status | Iowa City | United States | Unknown status |
This page is information, not medical advice. Discuss any trial with your doctor.