NCT06560346Withdrawn
Understanding the Natural History Early in the Course or Presentation of Friedreich Ataxia
Understanding the Natural History Early in the Course or Presentation of Friedreich Ataxia (EARLY-FA); Evaluating New Clinical Outcome Assessments in Children With Friedreich Ataxia to Facilitate Clinical Trial Design.
Source: ClinicalTrials.gov · Last updated 8 Jun 2025
Reason given: Lack of Funding
Brief summary (registry, in English)
Multicenter, prospective, observational natural history and outcome measure study of children and young adults with Friedreich ataxia.
- Status (registry)
- Withdrawn
- Study type
- Observational
- Enrollment
- 0 (actual)
- First submitted
- 15 Aug 2024
- Start date
- 1 May 2025
- Primary completion date
- 1 Dec 2028
- Lead sponsor
- Friedreich's Ataxia Research Alliance
- Diseases
- Friedreich ataxia
- NCT number
- NCT06560346
Who cannot take part
Copied verbatim from ClinicalTrials.gov and grouped by topic. Only the trial team decides who can take part.
Other illness
- Diagnosis of non-FA medical or other condition that in the opinion of the investigator would interfere with the conduct and assessments of the study or be confounding and contraindication to participation.
- Diagnosis of a medical condition that in the opinion of the investigator could be confounding and contraindication to participation
Other
- Pregnant female participants
- Unable to provide informed consent.
- Family risk for FA with unknown status
- Unable to provide informed consent
Who the study is looking for
- Genetic diagnosis of Friedreich Ataxia
- Ages 4-21 years at enrollment
- Enrollment in the UNIFAI study and ability to have simultaneous visits for both UNIFAI and EARLY-FA
- Informed consent must be obtained for all participants:
- For underage participants, they and the parent/ legally authorized representative have to sign the informed consent form, child assent (if applicable)
- Persons who are not legally competent require the informed consent of their legally authorized representative
- Ages 4-21 years at enrollment
- Matching criteria to an enrolled participant with FA (age, sex and educational status)
- Informed consent must be obtained for all participants:
- For underage participants, they and the parent/ legally authorized representative have to sign the informed consent form, child assent (if applicable)
- Persons who are not legally competent require the informed consent of their legally authorized representative
Age in the registry: 4 years to 21 years · Sex: All · Accepts healthy volunteers
Sites (7)
Sites in registry order. Save your city in your profile to sort them by distance.
| Site | City | Country | Site status |
|---|---|---|---|
| Murdoch Childrens Research Institute | Parkville | Australia | Unknown status |
| McGill University Health Centre - Montreal Neurological Institute | Montreal | Canada | Unknown status |
| University Hospital Aachen, Dept. of Neurology | Aachen | Germany | Unknown status |
| Bambino Gesù Children's Hospital, Department of Neurosciences | Roma | Italy | Unknown status |
| University of Iowa Stead Family Children's Hospital | Iowa City | United States | Unknown status |
| St. Jude Children's Research Hospital | Memphis | United States | Unknown status |
| Children's Hospital of Philadelphia | Philadelphia | United States | Unknown status |
This page is information, not medical advice. Discuss any trial with your doctor.