NCT07231549Recruiting
CuidAME: Longitudinal Data Collection From Patients With Spinal Muscular Atrophy in Spain
Source: ClinicalTrials.gov · Last updated 17 Nov 2025
Brief summary (registry, in English)
The goal of this observational study is to set up a longitudinal data collection study to perform a long-term follow-up of SMA patients in a real-world setting, and to standardise and homogenize the data collection process for SMA patient's data. Treated and untreated patients will be followed based on the routine clinical practice schedule.
- Status (registry)
- Recruiting
- Study type
- Observational
- Enrollment
- 1000 (estimated)
- First submitted
- 17 Jun 2025
- Start date
- 5 May 2020
- Primary completion date
- Dec 2026
- Lead sponsor
- Fundació Sant Joan de Déu
- Diseases
- Spinal muscular atrophy
- NCT number
- NCT07231549
What you commit to
- Study type: Observational
- Planned participants: 1000
- From 5 May 2020 to the primary completion date, Dec 2026
- 1 site in 1 country
- Visits and tests: ask the trial team, the registry does not list them
Built from the registry fields of ClinicalTrials.gov. It describes the study, not your situation.
Who cannot take part
Copied verbatim from ClinicalTrials.gov and grouped by topic. Only the trial team decides who can take part.
Other
- Further types of SMA (non-5q SMA).
- Patient without legal capacity who cannot understand the nature, significance, and consequences of the project.
Who the study is looking for
- Genetically confirmed 5q SMA
- Patient or caregivers written informed consent has been obtained (except for paediatric patients deceased).
Sex: All · Does not accept healthy volunteers
Sites (1)
Sites in registry order. Pick your city on the disease page to sort them by distance.
| Site | City | Country | Site status |
|---|---|---|---|
| Hospital Sant Joan De Deu Coordinator of this site? Confirm its status | Esplugues de Llobregat | Spain | Recruiting |
This page is information, not medical advice. Discuss any trial with your doctor.