NCT07373639Recruiting
A Long-term Follow-up Study in Patients Who Received BEAM-101
A Long-term Follow-up Study in Patients With Hemoglobinopathy Who Received Autologous CD34+ Edited Hematopoietic Stem Cells
Source: ClinicalTrials.gov · Last updated 28 Jan 2026
Brief summary (registry, in English)
This is a Long-term Follow-up (LTFU) study in patients who received BEAM-101 in the parent study (Study BTX-AUT-001). Eligible patients who received BEAM-101 will be asked to participate in this LTFU study prior to completing Study BTX-AUT-001. Patients who enter into this study will be followed for 13 years (a total of 15 years after receiving BEAM-101).
- Status (registry)
- Recruiting
- Study type
- Observational
- Enrollment
- 50 (estimated)
- First submitted
- 6 Jan 2026
- Start date
- 15 Dec 2025
- Primary completion date
- 12 Feb 2043
- Lead sponsor
- Beam Therapeutics Inc.
- Diseases
- Sickle cell disease
- NCT number
- NCT07373639
What you commit to
- Study type: Observational
- Planned participants: 50
- From 15 Dec 2025 to the primary completion date, 12 Feb 2043
- 17 sites in 1 country
- Visits and tests: ask the trial team, the registry does not list them
Built from the registry fields of ClinicalTrials.gov. It describes the study, not your situation.
Who cannot take part
Copied verbatim from ClinicalTrials.gov and grouped by topic. Only the trial team decides who can take part.
Other
- There are no exclusion criteria for this study.
Who the study is looking for
- Have received BEAM-101 in Study BTX-AUT-001 and are in the process of completing that study's end-of-study (EOS) visit.
- Provide signed, written informed consent according to local institutional review board (IRB)/independent ethics committee (IEC) and institutional requirements.
Age in the registry: 14 years to 37 years · Sex: All · Does not accept healthy volunteers
Sites (17)
Sites in registry order. Pick your city on the disease page to sort them by distance.
| Site | City | Country | Site status |
|---|---|---|---|
| Children's Healthcare of Atlanta - Aflac Cancer and Blood Disorders Center- Egleston Coordinator of this site? Confirm its status | Atlanta | United States | Not yet recruiting |
| University of Alabama at Birmingham Coordinator of this site? Confirm its status | Birmingham | United States | Not yet recruiting |
| Boston Children's Hospital Coordinator of this site? Confirm its status | Boston | United States | Recruiting |
| Medical University of South Carolina Coordinator of this site? Confirm its status | Charleston | United States | Not yet recruiting |
| University Hospitals Clevland Medical Center Coordinator of this site? Confirm its status | Cleveland | United States | Not yet recruiting |
| The Clevland Clinic Foundation Coordinator of this site? Confirm its status | Cleveland | United States | Not yet recruiting |
| Henry Ford Cancer Center Coordinator of this site? Confirm its status | Detroit | United States | Not yet recruiting |
| Hackensack University Medical Center Coordinator of this site? Confirm its status | Hackensack | United States | Not yet recruiting |
| Mayo Clinic Florida Coordinator of this site? Confirm its status | Jacksonville | United States | Not yet recruiting |
| St. Jude Children's Research Hospital Coordinator of this site? Confirm its status | Memphis | United States | Not yet recruiting |
| Medical College of Wisconsin Coordinator of this site? Confirm its status | Milwaukee | United States | Not yet recruiting |
| University of Minnesota Coordinator of this site? Confirm its status | Minneapolis | United States | Not yet recruiting |
| The Children's Hospital at TriStar Centennial Coordinator of this site? Confirm its status | Nashville | United States | Not yet recruiting |
| Columbia University Irving Medical Center Coordinator of this site? Confirm its status | New York | United States | Not yet recruiting |
| Children's Hospital of Philadelphia Coordinator of this site? Confirm its status | Philadelphia | United States | Not yet recruiting |
| Phoenix Children s Hospital Coordinator of this site? Confirm its status | Phoenix | United States | Not yet recruiting |
| Washington University School of Medicine in St. Louis Coordinator of this site? Confirm its status | St Louis | United States | Not yet recruiting |
This page is information, not medical advice. Discuss any trial with your doctor.