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NCT07373639Recruiting

A Long-term Follow-up Study in Patients Who Received BEAM-101

A Long-term Follow-up Study in Patients With Hemoglobinopathy Who Received Autologous CD34+ Edited Hematopoietic Stem Cells

Source: ClinicalTrials.gov · Last updated 28 Jan 2026

Brief summary (registry, in English)

This is a Long-term Follow-up (LTFU) study in patients who received BEAM-101 in the parent study (Study BTX-AUT-001). Eligible patients who received BEAM-101 will be asked to participate in this LTFU study prior to completing Study BTX-AUT-001. Patients who enter into this study will be followed for 13 years (a total of 15 years after receiving BEAM-101).

Status (registry)
Recruiting
Study type
Observational
Enrollment
50 (estimated)
First submitted
6 Jan 2026
Start date
15 Dec 2025
Primary completion date
12 Feb 2043
Lead sponsor
Beam Therapeutics Inc.
NCT number
NCT07373639

What you commit to

  • Study type: Observational
  • Planned participants: 50
  • From 15 Dec 2025 to the primary completion date, 12 Feb 2043
  • 17 sites in 1 country
  • Visits and tests: ask the trial team, the registry does not list them

Built from the registry fields of ClinicalTrials.gov. It describes the study, not your situation.

Who cannot take part

Copied verbatim from ClinicalTrials.gov and grouped by topic. Only the trial team decides who can take part.

Other

  • There are no exclusion criteria for this study.

Who the study is looking for

  • Have received BEAM-101 in Study BTX-AUT-001 and are in the process of completing that study's end-of-study (EOS) visit.
  • Provide signed, written informed consent according to local institutional review board (IRB)/independent ethics committee (IEC) and institutional requirements.

Age in the registry: 14 years to 37 years · Sex: All · Does not accept healthy volunteers

Full criteria on ClinicalTrials.gov

Sites (17)

Sites in registry order. Pick your city on the disease page to sort them by distance.

SiteCityCountrySite status
Children's Healthcare of Atlanta - Aflac Cancer and Blood Disorders Center- Egleston
Coordinator of this site? Confirm its status
AtlantaUnited StatesNot yet recruiting
University of Alabama at Birmingham
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BirminghamUnited StatesNot yet recruiting
Boston Children's Hospital
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BostonUnited StatesRecruiting
Medical University of South Carolina
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CharlestonUnited StatesNot yet recruiting
University Hospitals Clevland Medical Center
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ClevelandUnited StatesNot yet recruiting
The Clevland Clinic Foundation
Coordinator of this site? Confirm its status
ClevelandUnited StatesNot yet recruiting
Henry Ford Cancer Center
Coordinator of this site? Confirm its status
DetroitUnited StatesNot yet recruiting
Hackensack University Medical Center
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HackensackUnited StatesNot yet recruiting
Mayo Clinic Florida
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JacksonvilleUnited StatesNot yet recruiting
St. Jude Children's Research Hospital
Coordinator of this site? Confirm its status
MemphisUnited StatesNot yet recruiting
Medical College of Wisconsin
Coordinator of this site? Confirm its status
MilwaukeeUnited StatesNot yet recruiting
University of Minnesota
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MinneapolisUnited StatesNot yet recruiting
The Children's Hospital at TriStar Centennial
Coordinator of this site? Confirm its status
NashvilleUnited StatesNot yet recruiting
Columbia University Irving Medical Center
Coordinator of this site? Confirm its status
New YorkUnited StatesNot yet recruiting
Children's Hospital of Philadelphia
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PhiladelphiaUnited StatesNot yet recruiting
Phoenix Children s Hospital
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PhoenixUnited StatesNot yet recruiting
Washington University School of Medicine in St. Louis
Coordinator of this site? Confirm its status
St LouisUnited StatesNot yet recruiting

This page is information, not medical advice. Discuss any trial with your doctor.