Duchenne muscular dystrophy: open trials in France

17 open trials have a site in France. Registry data; only the trial team decides who can take part.

2023-504520-26-00
Study in which all the patients take the same investigational drug with the aim of evaluate the long-term safety, tolerability, and efficacy of GIVINOSTAT in all the patients affected with Duchenne Muscolar Dystrophy who have been already treated in one of the GIVINOSTAT studies in the past
Trial Treatment · Phase 3 · Italfarmaco S.p.A.
Centre Hospitalier Universitaire De Lille, Lille Cedex · Centre Hospitalier Regional De Marseille, Marseille · Centre Hospitalier Universitaire de Nantes, Nantes · Trousseau Hospital, Paris
Registry updated 2026-11-06
NCT07740057
Multimodal Study About Absence of Dp140 in Becker Muscular Dystrophy: Brain-muscle Imaging, Cognition and Muscle Function
Research · Institut de Myologie, France
Institute of Mythology, Paris
Registry updated 2026-11-03
NCT06833489
Transcriptomic Analysis to Put an End to Misdiagnosis in Patients With Rare Muscle Diseases
Trial Treatment · Assistance Publique Hopitaux De Marseille
Hôpital Timone, Marseille
Registry updated 2026-10-28
NCT06147414
Development of Non-Invasive Prenatal Diagnosis for Single Gene Disorders
Research · Assistance Publique - Hôpitaux de Paris
Hôpital Cochin, Maternité Port-Royal, service de Gynécologie obstétrique, Paris
Registry updated 2026-10-21
NCT07587242
A Phase 3 Study to Evaluate the Safety and Efficacy of AOC 1044 (Also Referred to as Delpacibart Zotadirsen) in Participants With DMD With Gene Mutations Amenable to Exon 44 Skipping
Trial Treatment · Phase 3 · Avidity Biosciences, Inc.
CHU de Nantes - Hôtel Dieu, Nantes · AP-HP Hospital Armand-Trousseau, Paris
Registry updated 2026-10-13
NCT07856329
A Clinical Study to Assess Safety, Efficacy and Pharmacodynamic Profile of GNT0004 in Duchenne Muscular Dystrophy
Trial Treatment · Phase 2/3 · Genethon
University Of Bordeaux, Bordeaux Cedex · Centre Hospitalier Regional Et Universitaire De Brest, Brest Cedex 2 · Hospices Civils de Lyon, Bron · Centre Hospitalier Universitaire De Lille, Lille Cedex · Centre Hospitalier Universitaire de Montpellier, Montpellier · Association Institut De Myologie, Paris · Les Hopitaux Universitaires De Strasbourg, Strasbourg Cedex 2
Registry updated 2026-10-13
NCT07160634
A Study of SGT-003 Gene Therapy in Ambulant Males With Duchenne Muscular Dystrophy (IMPACT DUCHENNE)
Trial Treatment · Phase 3 · Solid Biosciences Inc.
Assistance Publique Hopitaux de Paris, Paris · Les Hopitaux Universitaires De Strasbourg, Strasbourg Cedex 2
Registry updated 2026-09-28
NCT06066580
Open-Label Extension of EDG-5506 in Participants With Becker Muscular Dystrophy
Trial Treatment · Phase 2 · Edgewise Therapeutics, Inc.
Centre de Reference des Maladies Neuromusculaires et de la SLA - AP-HM Hopital de La Timone, Marseille · CHU de Nantes, Nantes · CHU de Nice - Hopital Pasteur 2 - Centre de reference des Maladies Neuromusculaires, Nice · AP-HP Hopital Pitie-Salpetriere, Paris
Registry updated 2026-09-17
NCT07037862
A Study in Participants With Duchenne Muscular Dystrophy Amenable to Exon 44 Skipping to Evaluate the Safety and Efficacy of ENTR-601-44
Trial Treatment · Phase 1/2 · Entrada Therapeutics, Inc.
Trousseau Hospital, Paris · Centre Hospitalier Universitaire De Toulouse, Toulouse Cedex 9
Registry updated 2026-08-13
NCT07038824
A Study in Participants With Duchenne Muscular Dystrophy Amenable to Exon 45 Skipping to Evaluate the Safety and Efficacy of ENTR-601-45
Trial Treatment · Phase 1/2 · Entrada Therapeutics, Inc.
Hospices Civils de Lyon, Bron · Trousseau Hospital, Paris · Centre Hospitalier Universitaire De Toulouse, Toulouse Cedex 9
Registry updated 2026-08-13
NCT05933057
Efficacy, Safety and Tolerability of Givinostat in Non-ambulant Patients With Duchenne Muscular Dystrophy
Trial Treatment · Phase 3 · Italfarmaco
Centre Hospitalier Universitaire De Lille, Lille Cedex · Assistance Publique Hôpitaux de Marseille, Marseille · Association Institut De Myologie, Paris
Registry updated 2026-07-24
NCT07378553
Multiparametric Ultrafast Ultrasound Biomarkers for Duchenne and Becker Muscular Dystrophies
Research · Nantes University Hospital
CHU de Nantes, Nantes
Registry updated 2026-06-24
2025-523087-20-00
A Phase 3, Randomized, Double-Blind, Placebo-Controlled, Global Study with an Open-Label Extension to Evaluate the Efficacy and Safety of Intravenous AOC 1044 (delpacibart zotadirsen) for the Treatment of DMD with Gene Mutations Amenable to Exon 44 Skipping
Trial Treatment · Phase 3 · Avidity Biosciences Inc.
Hospital Hotel Dieu, Nantes · Assistance Publique Hopitaux de Paris, Paris
Registry updated 2026-05-27
2022-500703-49-01
Phase 1/2a study to Evaluate the Safety, Pharmacokinetics, and Pharmacodynamics of SQY51 in Paediatric and Adult Patients with a Genetically Confirmed Diagnosis of Duchenne Muscular Dystrophy
Trial Treatment · Phase 1/2 · Sqy Therapeutics
Assistance Publique Hopitaux De Paris, Garches
Registry updated 2026-02-27
NCT07415837
Evaluation of the Role of miR-1 in the Pathogenesis and as a Biomarker in Muscular Dystrophies and Congenital Myopathies
Trial Treatment · University Hospital, Clermont-Ferrand
CHU de Clermont-Ferrand, Clermont-Ferrand
Registry updated 2026-02-25
NCT03882827
Natural History of Duchenne Muscular Dystrophy
Research · Genethon
University Hospital of Bordeaux, Bordeaux · Brest University Hospital Centre, Brest · Hôpital Femme Mère Enfant, Bron · CHU Lille, Lille · Hopital La Timone - Enfants, Marseille · Centre Hospitalier Universitaire - Hôpital Gui de Chauliac, Montpellier · Hôpital Armand-Trousseau, Paris · Hopital Hautepierre, Strasbourg
Registry updated 2026-02-12
NCT03373968
Givinostat in Duchenne's Muscular Dystrophy Long-term Safety and Tolerability Study
Trial Treatment · Phase 2/3 · Italfarmaco
CHU de Nantes - Hotel-Dieu - Hopital Nord Laennec, rez-de-chausse haut ail Ouest, Nantes · Hôpital Armand Trousseau I-Motion - Plateforme d'essais cliniques pédiatriques Bâtiment Lemariey - Porte 20 * 2ème étage 26 Avenue du Dr Arnold Nette, Paris
Registry updated 2026-01-21

All Duchenne muscular dystrophy trials and the map

This page is not medical advice. Talk to your doctor before contacting a trial.

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