Fabry disease: open trials in Germany

• NCT07778667

  A Study to Learn How Well Lucerastat Works and How Safe it is in Untreated Adult Male Participants With Fabry Disease

  Trial Treatment · Phase 3 · Idorsia Pharmaceuticals Ltd.

  Charite Universitaetsmedizin Berlin KöR, Berlin · Universitaetsklinikum Wuerzburg AöR, Wuerzburg

  Registry updated 2026-11-03

• NCT06904261

  A Study of Migalastat in Pediatric Subjects (2 to <12 Yrs) With Fabry Disease and Amenable GLA Variants

  Trial Treatment · Phase 3 · Amicus Therapeutics

  Universitäetsklinikum Müenster (UKM) Klinik für Kinder- und Jugendmedizin - Allgemeine Paediatrie, Münster

  Registry updated 2026-10-22

• NCT00196742

  Fabry Disease Registry & Pregnancy Sub-registry

  Research · Genzyme, a Sanofi Company

  Berlin · Giessen · Münster · Würzburg

  Registry updated 2026-10-14

• 2025-521244-38-00

  An Open-label Study of the Safety, Pharmacokinetics, Pharmacodynamics, and Efficacy of 12-month Treatment with Migalastat in Pediatric Subjects (aged 2 to < 12 years) with Fabry Disease and Amenable GLA Variants

  Trial Treatment · Phase 3 · Amicus Therapeutics Inc.

  Universitaetsklinikum Muenster AöR, Muenster

  Registry updated 2026-04-24

• NCT06941025

  Maternal and Postnatal Outcomes Study (MOS): A Global Observational Registry Assessing the Safety of Elfabrio® in Women With Fabry Disease and Their Infants During Pregnancy and Breastfeeding

  Research · Chiesi Farmaceutici S.p.A.

  No physical study sites - Decentralized, web-based registry, Berlin

  Registry updated 2026-03-19

• NCT06758648

  Characterizing the Retinal Microvasculature in Patients with Fabry Disease: a Prospective Observational Study

  Research · Technical University of Munich

  Department of nephrology, Klinikum rechts der Isar, München

  Registry updated 2025-01-06

• NCT03362164

  Evaluation of HEArt invoLvement in Patients With FABRY Disease

  Research · Wuerzburg University Hospital

  Wuerzburg University Hospital, Würzburg

  Registry updated 2022-07-07

All Fabry disease trials and the map

This page is not medical advice. Talk to your doctor before contacting a trial.

Report an error