Fabry disease: open trials in United Kingdom

• NCT07778667

  A Study to Learn How Well Lucerastat Works and How Safe it is in Untreated Adult Male Participants With Fabry Disease

  Trial Treatment · Phase 3 · Idorsia Pharmaceuticals Ltd.

  The Royal Free London NHS Foundation Trust - The Royal Free, London · Salford Royal NHS Foundation Trust part of the Northern Care, Salford

  Registry updated 2026-11-03

• NCT06904261

  A Study of Migalastat in Pediatric Subjects (2 to <12 Yrs) With Fabry Disease and Amenable GLA Variants

  Trial Treatment · Phase 3 · Amicus Therapeutics

  Great Ormond Street Hospital For Children NHS Foundation Trust, London · Manchester University NHS Foundation Trust, Manchester

  Registry updated 2026-10-22

• NCT00196742

  Fabry Disease Registry & Pregnancy Sub-registry

  Research · Genzyme, a Sanofi Company

  Belfast · Birmingham · Cambridge · London · London · London · Manchester · Salford

  Registry updated 2026-10-14

• NCT06328608

  A Study to Learn About the Safety and Effects of the Study Drug PRX-102 in Children and Adolescents With Fabry Disease

  Trial Treatment · Phase 2/3 · Chiesi Farmaceutici S.p.A.

  Great Ormond Street Hospital For Children NHS Foundation Trust, London

  Registry updated 2026-08-10

• NCT06941025

  Maternal and Postnatal Outcomes Study (MOS): A Global Observational Registry Assessing the Safety of Elfabrio® in Women With Fabry Disease and Their Infants During Pregnancy and Breastfeeding

  Research · Chiesi Farmaceutici S.p.A.

  No physical study sites - Decentralized, web-based registry, London

  Registry updated 2026-03-19

• NCT06663358

  A Multi-Country Observational Study of Safety and Effectiveness of Elfabrio® in Fabry Patients

  Research · Chiesi Farmaceutici S.p.A.

  University Hospitals Birmingham NHS Foundation Trust, Queen Elizabeth Hospital, Edgbaston · The Royal Free Hospital, London · Salford Royal, Salford

  Registry updated 2025-11-14

• NCT06065852

  National Registry of Rare Kidney Diseases

  Research · UK Kidney Association

  Zoe Plummer, Bristol

  Registry updated 2023-10-04

All Fabry disease trials and the map

This page is not medical advice. Talk to your doctor before contacting a trial.

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