Gaucher disease: open trials in Netherlands

• 2026-527117-33-00

  ONCE: Once daily eliglustat in stable CYP2D6 intermediate and extensive metabolizers with Gaucher disease type 1

  Trial Treatment · Phase 4 · Amsterdam UMC Stichting

  Amsterdam UMC Research B.V., Amsterdam

  Registry updated 2026-10-22

• NCT00358943

  International Collaborative Gaucher Group (ICGG) Gaucher Disease Registry & Pregnancy Sub-registry

  Research · Genzyme, a Sanofi Company

  Amsterdam · Amsterdam

  Registry updated 2026-10-14

• 2024-514012-28-00

  Effectiveness of ambroxol in children and adults with Gaucher disease 3: n-of-1 series

  Trial Treatment · Phase 3 · Amsterdam UMC Stichting

  Amsterdam UMC Stichting, Amsterdam

  Registry updated 2024-11-25

All Gaucher disease trials and the map

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