Haemophilia: open trials in Australia

9 open trials have a site in Australia. Registry data; only the trial team decides who can take part.

NCT07416604
A Clinical Study to Evaluate the Effects of NXT007 Compared to Emicizumab Prophylaxis in People With Hemophilia A
Trial Treatment · Phase 3 · Hoffmann-La Roche
Royal Prince Alfred Hospital, Camperdown · The Alfred Hospital, Melbourne · Royal Children's Hospital Melbourne - PIN, Parkville
Registry updated 2026-11-03
NCT07830732
A Research Study Investigating Denecimig (Mim8) in Adults With Acquired Haemophilia A
Trial Treatment · Phase 3 · Novo Nordisk A/S
Royal Prince Alfred Hospital - Department of Haematology, Camperdown · Royal Brisbane and Women's Hospital - Integrated Cancer Research (I-CARE), Herston · The Alfred - Cancer Trials, Melbourne
Registry updated 2026-10-28
NCT05145127
Open-Label Extension Study of Marstacimab in Hemophilia Participants With or Without Inhibitors
Trial Treatment · Phase 3 · Pfizer
Royal Children's Hospital, Melbourne
Registry updated 2026-10-26
NCT06379789
A Study to Investigate the Safety and Effectiveness of a Coagulation Factor IX Gene Insertion Therapy (REGV131-LNP1265) in Pediatric, Adolescent and Adult Participants With Hemophilia B
Trial Treatment · Phase 1/2 · Regeneron Pharmaceuticals
Royal Adelaide Hospital, Adelaide · Royal Prince Alfred Hospital, Haemophilia Treatment Centre, Camperdown · Royal Brisbane and Women's Hospital, Herston · Alfred Hospital, Melbourne
Registry updated 2026-10-21
NCT07080905
Phase 3, Open-label, Single-dose Study of CSL222 in Adolescent Male Subjects (≥ 12 to < 18 Years of Age) With Severe or Moderately Severe Hemophilia B
Trial Treatment · Phase 3 · CSL Behring
Queensland Children's Hospital, Brisbane · The Children's Hospital at Westmead, Westmead
Registry updated 2026-10-20
NCT05611801
A Clinical Trial of Study Medicine (Marstacimab) in Pediatric Patients With Hemophilia A or Hemophilia B
Trial Treatment · Phase 3 · Pfizer
Murdoch Children's Research Institute, Parkville
Registry updated 2026-10-14
NCT05568719
Safety and Effectiveness of Giroctocogene Fitelparvovec or Fidanacogene Elaparvovec in Patients With Hemophilia A or B Respectively
Trial Treatment · Phase 3 · Pfizer
Royal Prince Alfred Hospital, Camperdown · Sydney Local Health District (RPAH Zone), Camperdown · The Alfred Hospital, Melbourne
Registry updated 2026-10-07
NCT06003387
Efficacy and Safety of CSL222 (Etranacogene Dezaparvovec) Gene Therapy in Adults With Hemophilia B With Pretreatment Adeno-associated Virus Serotype 5 (AAV5) Neutralizing Antibodies (Nabs)
Trial Treatment · Phase 3 · CSL Behring
Royal Adelaide Hospital, Adelaide · Royal Prince Alfred Hospital, Camperdown · Royal Brisbane Hospital, Herston · The Alfred Hospital, Melbourne
Registry updated 2026-08-27
NCT05768386
A Long-Term Follow-Up Study in Severe Hemophilia A Subjects Who Received BMN 270 in a Prior BioMarin Clinical Trial (270-401)
Research · Phase 4 · BioMarin Pharmaceutical
Royal Adelaide Hospital, Adelaide · Royal Brisbane and Women's Hospital, Herston · The Alfred Hospital, Melbourne · Fiona Stanley Hospital, Murdoch · Royal Prince Alfred Hospital, Institute of Haematology, Sydney
Registry updated 2026-01-12

All Haemophilia trials and the map

This page is not medical advice. Talk to your doctor before contacting a trial.

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