Pompe disease: open trials in Belgium

• NCT00231400

  Pompe Disease Registry Protocol

  Research · Genzyme, a Sanofi Company

  Antwerp · Bruges · Brussels · Brussels · Edegem · Ghent · Gosselies · Leuven · Leuven

  Registry updated 2026-10-28

• 2025-522146-40-00

  A phase 2, randomized, double-blind study of S-606001 as an add-on to enzyme replacement therapy in patients with late-onset Pompe disease.

  Trial Treatment · Phase 2 · Shionogi B.V.

  UZ Leuven, Leuven

  Registry updated 2026-09-18

• NCT07123155

  Study of S-606001 as an Add-on to Enzyme Replacement Therapy (ERT) in Participants With Late-onset Pompe Disease (LOPD)

  Trial Treatment · Phase 2 · Shionogi

  UZ Leuven, Leuven

  Registry updated 2026-06-23

• NCT00567073

  Pompe Pregnancy Sub-Registry

  Research · Genzyme, a Sanofi Company

  Ghent

  Registry updated 2026-04-16

• NCT06121011

  A Global Prospective Observational Registry of Patients With Pompe Disease

  Research · Amicus Therapeutics

  Laboratory for Muscle Diseases and Neuropathies, Leuven

  Registry updated 2026-03-10

• NCT07136844

  Gait Analysis Parameter and Upper Limb Evaluation in Adult Patients With Neurological or Metabolic Pathology

  Trial Treatment · Centre Hospitalier Universitaire de Liege

  Centre de référence des maladies neuromusculaire, Centre Hospitalier Régional de la Citadelle, Liège

  Registry updated 2025-08-22

All Pompe disease trials and the map

This page is not medical advice. Talk to your doctor before contacting a trial.

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