Pompe disease: open trials in China

• NCT00231400

  Pompe Disease Registry Protocol

  Research · Genzyme, a Sanofi Company

  Beijing · Beijing · Beijing · Guangzhou · Jinan · Jinan · Shanghai · Shanghai

  Registry updated 2026-10-28

• NCT06666413

  China Post-approval Commitment (PAC) Study of Avalglucosidase Alfa in Participants With IOPD

  Trial Treatment · Phase 4 · Genzyme, a Sanofi Company

  Shanghai

  Registry updated 2026-03-23

• NCT06391736

  Evaluation of the Safety and Efficacy of Late-onset Pompe Disease Gene Therapy Drug

  Trial Treatment · Phase 1/2 · GeneCradle Inc

  Chinese PLA General Hospital, Beijing

  Registry updated 2025-07-03

• NCT06178432

  Evaluation of the Safety, Tolerability and Efficacy of Gene Therapy Drug for Late Onset Pompe Disease (LOPD)

  Trial Treatment · Early phase 1 · Huashan Hospital

  Huashan Hospital of Fudan University, Shanghai

  Registry updated 2023-12-21

All Pompe disease trials and the map

This page is not medical advice. Talk to your doctor before contacting a trial.

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