Pompe disease: open trials in Germany

9 open trials have a site in Germany. Registry data; only the trial team decides who can take part.

NCT00231400
Pompe Disease Registry Protocol
Research · Genzyme, a Sanofi Company
Berlin · Berlin · Berlin · Bochum · Bonn · Freiburg im Breisgau · Giessen · Halle · Hamburg · Mainz · Munich · Münster
Registry updated 2026-10-28
2025-522146-40-00
A phase 2, randomized, double-blind study of S-606001 as an add-on to enzyme replacement therapy in patients with late-onset Pompe disease.
Trial Treatment · Phase 2 · Shionogi B.V.
Martin-Luther-Universitaet Halle-Wittenberg, Halle (Saale) · SphinCS GmbH, Hochheim Am Main · LMU Klinikum Muenchen AöR, Munich
Registry updated 2026-09-18
NCT07354724
A Study to Evaluate the Safety, Pharmacokinetics, and Pharmacodynamics of DNL952 in Adult Participants With Late-Onset Pompe Disease
Trial Treatment · Phase 1 · Denali Therapeutics Inc.
SphinCS GmbH, Hochheim Am Main
Registry updated 2026-08-17
NCT07123155
Study of S-606001 as an Add-on to Enzyme Replacement Therapy (ERT) in Participants With Late-onset Pompe Disease (LOPD)
Trial Treatment · Phase 2 · Shionogi
Universitaetsklinikum Halle - Saale, Halle · SphinCS GmbH, Höchheim · Klinikum der Ludwig-Maximilians-Universitaet Muenchen, München
Registry updated 2026-06-23
NCT00567073
Pompe Pregnancy Sub-Registry
Research · Genzyme, a Sanofi Company
Bonn
Registry updated 2026-04-16
NCT06121011
A Global Prospective Observational Registry of Patients With Pompe Disease
Research · Amicus Therapeutics
Ruhr-Universität Bochum im St. Josef-Hospital, Bochum · SphinCS, Institute of Clinical Science in LSD, Höchheim · Universitätsklinikum Gießen und Marburg GmhH, Marburg · Universitat Munchen - Friedrich Baur Institut, München · Universitaetsklinikum Ulm, Ulm
Registry updated 2026-03-10
NCT04808505
A Study to Evaluate the Safety, Efficacy, PK, PD and Immunogenicity of Cipaglucosidase Alfa/Miglustat in IOPD Subjects Aged 0 to <18
Trial Treatment · Phase 3 · Amicus Therapeutics
Justus Liebig University Giessen, Giessen · Universitaetsklinikum Heidelberg AöR, Heidelberg · SphinCS GmbH, Hochheim Am Main · Universitaetsklinikum Muenster AöR, Münster
Registry updated 2026-01-22
NCT06605612
Development and Validation of the FBIndex to Determine the Risk of Falls for Patients With Neuromuscular Disorders
Research · LMU Klinikum
Friedrich-Baur-Institut, Neurologische Klinik und Poliklinik, LMU Klinikum, Ludwig-Maximilians-Universität München, München
Registry updated 2025-09-10
NCT07072676
The Use of Assistive Gait Devices Can Reduce the Risk of Falls in Patients With Neuromuscular Diseases Following a Training Period.
Trial Treatment · LMU Klinikum
Medical Park, Bad Feilnbach, Reithofpark, Bad Feilnbach
Registry updated 2025-07-18

All Pompe disease trials and the map

This page is not medical advice. Talk to your doctor before contacting a trial.

Report an error