Pompe disease: open trials in Denmark

• NCT00231400

  Pompe Disease Registry Protocol

  Research · Genzyme, a Sanofi Company

  Copenhagen

  Registry updated 2026-10-28

• 2025-522146-40-00

  A phase 2, randomized, double-blind study of S-606001 as an add-on to enzyme replacement therapy in patients with late-onset Pompe disease.

  Trial Treatment · Phase 2 · Shionogi B.V.

  Aarhus Universitethospital, Aarhus N

  Registry updated 2026-09-18

• NCT07123155

  Study of S-606001 as an Add-on to Enzyme Replacement Therapy (ERT) in Participants With Late-onset Pompe Disease (LOPD)

  Trial Treatment · Phase 2 · Shionogi

  Aarhus University Hospital, Aarhus

  Registry updated 2026-06-23

• NCT06121011

  A Global Prospective Observational Registry of Patients With Pompe Disease

  Research · Amicus Therapeutics

  Aarhus Universitets hospital, Aarhus C

  Registry updated 2026-03-10

• NCT04808505

  A Study to Evaluate the Safety, Efficacy, PK, PD and Immunogenicity of Cipaglucosidase Alfa/Miglustat in IOPD Subjects Aged 0 to <18

  Trial Treatment · Phase 3 · Amicus Therapeutics

  Copenhagen University Hospital, Copenhagen Oe

  Registry updated 2026-01-22

• 2023-508000-37-01

  GLYCOGEN RESPONSE TO ENZYME REPLACEMENT THERAPY IN POMPE DISEASE

  Trial Treatment · Phase 4 · Rigshospitalet

  Rigshospitalet, Copenhagen Oe

  Registry updated 2025-08-22

All Pompe disease trials and the map

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