Spinal muscular atrophy: open trials in Brazil

3 open trials have a site in Brazil. Registry data; only the trial team decides who can take part.

NCT07221669
A Study to Learn About Salanersen's (BIIB115) Effects on Movement and Its Safety When Given Before Symptoms Appear in Babies With Genetically Diagnosed Spinal Muscular Atrophy (SMA)
Trial Treatment · Phase 3 · Biogen
Hospital da Crianca de Brasilia, Distrito Federal · Hospital de Clinicas de Porto Alegre HCPA PPDS, Porto Alegre · PSEG Centro de Pesquisa Clinica, Sai Paula · Instituto Da Criança HC FMUSP, São Paulo
Registry updated 2026-10-23
NCT07070999
Study of Safety, Tolerability and Efficacy of GB221 in Infants With Spinal Muscular Atrophy Type 1
Trial Treatment · Phase 1/2 · Gemma Biotherapeutics
Hospital de Clinicas de Porto Alegre, Porto Alegre
Registry updated 2026-06-29
NCT06019637
A Long-term Safety Study in Brazilian Patients With a Diagnosis of Spinal Muscular Atrophy Treated With Zolgensma
Research · Novartis Pharmaceuticals
Curitiba · São Paulo
Registry updated 2025-01-15

This page is not medical advice. Talk to your doctor before contacting a trial.

A Study to Learn About Salanersen's (BIIB115) Effects on Movement and Its Safety When Given Before Symptoms Appear in Babies With Genetically Diagnosed Spinal Muscular Atrophy (SMA)