Spinal muscular atrophy: open trials in Canada

• NCT07287982

  A Study to Assess the Safety, Tolerability, Efficacy, Pharmacokinetics, and Immunogenicity of Intravenous Administration of ARGX-119 in Pediatric Participants Aged 5 to Less Than 18 Years With Spinal Muscular Atrophy

  Trial Treatment · Phase 2 · argenx

  University of Calgary - Alberta Children's Hospital, Calgary · The Hospital for Sick Children, Toronto · BC Children ' s Hospital, Vancouver

  Registry updated 2026-10-08

• NCT07846696

  An Open Label Individual Patient (OLIP)-02 Study of Nusinersen (BIIB058)

  Trial Treatment · Phase 3 · London Health Sciences Centre Research Institute OR Lawson Research Institute of St. Joseph's

  Children's Hospital London Health Sciences Centre, London

  Registry updated 2026-09-29

• NCT07838779

  An OLIP Study (Open Label Individual Patient) of Nusinersen in a Participant With Spinal Muscular Atrophy Who Previously Participated in an Investigational Study With Nusinersen

  Trial Treatment · London Health Sciences Centre Research Institute OR Lawson Research Institute of St. Joseph's

  Children's Hospital London Health Sciences Centre, London

  Registry updated 2026-09-24

• NCT06396325

  A Registry Based Randomized-Controlled Trial of an Upper Limb Exergaming Intervention for Children and Adolescents With Spinal Muscular Atrophy

  Trial Treatment · Maryam Oskoui, MD, MSc, FRCPC, FAAN

  Alberta Children's Hospital, Calgary · IWK Health Services, Halifax · Centre de readaptation Marie-Enfant, Montreal · Hospital for SickKids, Toronto · BC Children ' s Hospital, Vancouver

  Registry updated 2025-07-08

All Spinal muscular atrophy trials and the map

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