Spinal muscular atrophy: open trials in Japan

• NCT07221669

  A Study to Learn About Salanersen's (BIIB115) Effects on Movement and Its Safety When Given Before Symptoms Appear in Babies With Genetically Diagnosed Spinal Muscular Atrophy (SMA)

  Trial Treatment · Phase 3 · Biogen

  Japan Institute for Health Security National Center for Global Health and Medicine, Tokyo

  Registry updated 2026-10-23

• NCT07767890

  A Study of the Safety and Effectiveness of Onasemnogene Abeparvovec (Zolgensma) Intrathecal Injection in Spinal Muscular Atrophy Patients

  Research · Novartis Pharmaceuticals

  Fukuoka · Kodaira · Kyoto · Toyoake

  Registry updated 2026-10-22

• NCT04174157

  Registry of Patients With a Diagnosis of Spinal Muscular Atrophy (SMA)

  Research · Novartis Pharmaceuticals

  Chiba children's Hospital, Chiba · Fukui Prefectural Hospital, Fukui · Gifu Prefectural General Medical Center, Gifu · Hamamatsu University School of Medicine, University Hospital, Hamamatsu · Obihiro Kosei Hospital, Hokkaido · Nikko Memorial Hospital, Hokkaido · Kagawa University Hospital, Kita-gun · Kumamoto University Hospital, Kumamoto · Kurume University Hospital, Kurume-shi · Shiga Medical Center for Children, Moriyama-shi · Aichi Medical University Hospital, Nagakute-shi · Dokkyo Medical University Saitama Medical Center, Saitama · Sapporo Medical University Hospital, Sapporo · Miyagi Children's Hospital, Sendai · Jichi Medical University Hospital, Shimotsuke-shi · Tokyo Medical University Hospital, Shinjuku-ku · Center Hospital of the National Center for Global Health and Medicine, Shinjuku-Ku · Fujita Health University Hospital, Toyoake-shi · Kanagawa Children's Medical Center, Yokohama

  Registry updated 2025-01-31

All Spinal muscular atrophy trials and the map

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