Clinical trials

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25 trials

NCT07886879
Recruiting
Parkinson's Disease in Type 1 Gaucher Disease
Not applicable · United States · 1 site
Registry update: 5 Nov 2026
NCT07758816
Recruiting
Advancing Integrated Therapies for Gaucher Disease
Not applicable · United States · 1 site
Registry update: 11 Aug 2026
NCT07223944
Recruiting
A Gaucher Disease Gene Therapy Trial With FLT201
Phase 3 · Argentina, Australia, Brazil, Canada, Spain, United Kingdom, Israel, Saudi Arabia, United States · 32 sites
Registry update: 14 Oct 2026
2024-514012-28-00
Recruiting
Effectiveness of ambroxol in children and adults with Gaucher disease 3: n-of-1 series
Phase 3 · Netherlands · 1 site
Registry update: 25 Nov 2024
NCT06818838
Recruiting
A Clinical Study Evaluating LY-M001 Injection in the Treatment of Adult Patients With Type I Gaucher Disease
Phase 1/2 · China · 3 sites
Registry update: 26 Jan 2026
NCT06573723
Recruiting
Institutional Registry of Rare Diseases
Not applicable · Argentina · 1 site
Registry update: 14 Jan 2026
NCT06162338
Recruiting
A Study of the Safety and Preliminary Efficacy of LY-M001 Injection in the Treatment of Adult Patients With Gaucher Disease Type I
Not applicable · China · 1 site
Registry update: 14 Feb 2025
NCT05843552
Recruiting
Extracellular Vesicles as Potential Biomarkers and Therapeutic Target in Gaucher Disease
Not applicable · United States · 1 site
Registry update: 6 Apr 2026
NCT05992532
Recruiting
GammaGA: Prevalence of Acid Sphingomyelinase Deficiency Disease (ASMD) and Gaucher Disease in Patients With Monoclonal Gammopathies and/or Multiple Myeloma
Not applicable · Spain · 23 sites
Registry update: 11 Feb 2026
NCT06272149
Recruiting
An Exploratory Clinical Trial of VGN-R08b in Patients With Type II Gaucher Disease
Early phase 1 · China · 1 site
Registry update: 22 Feb 2024
NCT05586243
Recruiting
MAGNETIC RESONANCE SPECTROSCOPY BIOMARKERS IN TYPE 3 GAUCHER DISEASE (GD3)
Not applicable · United States · 1 site
Registry update: 4 Aug 2026
NCT05619900
Recruiting
Registry of Patients Diagnosed With Lysosomal Storage Diseases
Not applicable · United States · 1 site
Registry update: 8 Apr 2026
NCT04532047
Recruiting
PEARL (PrEnAtal Enzyme Replacement Therapy for Lysosomal Storage Disorders)
Phase 1 · United States · 1 site
Registry update: 17 Mar 2026
NCT04528355
Recruiting
Data Collection Study of Patients With Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT With RIC
Not applicable · United States · 1 site
Registry update: 13 Jan 2026
NCT04388969
Recruiting
World Data on Ambroxol for Patients With GD and GBA Related PD
Not applicable · Israel · 1 site
Registry update: 29 Apr 2026
NCT06151002
Recruiting
PD Frontline (Part of RAPSODI GD) Remote Assessment of People With Parkinson's
Not applicable · United Kingdom · 1 site
Registry update: 29 Oct 2026
NCT03190837
Recruiting
A Long-term Follow-up Study of Gaucher Disease
Not applicable · United States · 1 site
Registry update: 3 Sept 2026
NCT05253560
Recruiting
Prodromal Parkinsonian Features in GBA1 Mutation Carriers
Not applicable · Israel · 1 site
Registry update: 29 Apr 2026
NCT02437396
Recruiting
Oxidative Stress and Inflammatory Biomarkers in Gaucher Disease
Not applicable · United States · 1 site
Registry update: 4 Nov 2026
NCT01962415
Recruiting
Reduced Intensity Conditioning for Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT
Phase 2 · United States · 1 site
Registry update: 15 Dec 2025

Ordered by registry start date. Freshness and sponsorship never change the order.