Duchenne muscular dystrophy: what we know about treatments people ask about
How far testing has got for each one in Duchenne muscular dystrophy. This is what we know today, not advice.
How far testing has got
The step says how far testing has got, not that it works.
- Large trialsMetforminTested in large studies that compare groups of patients. This says how far testing has got, not that it works.Phase 3 or randomised controlled trial on record. The rung shows the stage reached; the result is listed separately.
- First trials in peopleHyperthermiaFirst small studies in people, mainly to check safety and the dose.Phase 1, early Phase 1 or Phase 1/2 trial on record.
- First trials in peopleMelatoninFirst small studies in people, mainly to check safety and the dose.Phase 1, early Phase 1 or Phase 1/2 trial on record.
- First trials in peopleStatinsFirst small studies in people, mainly to check safety and the dose.Phase 1, early Phase 1 or Phase 1/2 trial on record.
- Reports in peopleFasting and fasting-mimicking dietSingle case reports or observations in people. These cannot show whether it helps.Case reports, observational data, or pooled data without a reported benefit.
- Reports in peopleVitamin DSingle case reports or observations in people. These cannot show whether it helps.Case reports, observational data, or pooled data without a reported benefit.
- Animal studies onlyCannabis and cannabinoids (CBD, THC)Tested in animals only. Many things that work in animals do not work in people.In-vivo animal studies only.
- Animal studies onlyCurcumin (turmeric)Tested in animals only. Many things that work in animals do not work in people.In-vivo animal studies only.
- Animal studies onlyHigh-dose vitamin CTested in animals only. Many things that work in animals do not work in people.In-vivo animal studies only.
- Animal studies onlyKetogenic dietTested in animals only. Many things that work in animals do not work in people.In-vivo animal studies only.
Not medical advice. Talk to the care team before changing treatment. Thinking of paying for it? Read this first