Friedreich ataxia: what we know about treatments people ask about
How far testing has got for each one in Friedreich ataxia. This is what we know today, not advice.
How far testing has got
The step says how far testing has got, not that it works.
- First trials in peopleHyperthermiaFirst small studies in people, mainly to check safety and the dose.Phase 1, early Phase 1 or Phase 1/2 trial on record.
- Reports in peopleMetforminSingle case reports or observations in people. These cannot show whether it helps.Case reports, observational data, or pooled data without a reported benefit.
- Reports in peopleVitamin DSingle case reports or observations in people. These cannot show whether it helps.Case reports, observational data, or pooled data without a reported benefit.
- Lab studies onlyHigh-dose vitamin CTested on cells in a lab dish only.In-vitro and cell-line studies only.
Not medical advice. Talk to the care team before changing treatment. Thinking of paying for it? Read this first