Written from the studies on PubMed, searched on 11 Nov 2026. Every number below comes from a study listed under Sources.
What people read
Posts online say that Stem cell treatment helps with Fabry disease.
What has been studied
- 0In people
- 4In animals
- 22Only in the lab
What the studies found
Stem cell treatment has been studied for Fabry disease in animals, not yet in people.
We found 34 published papers on Stem cell treatment and Fabry disease. They were published between 2002 and 2026.
0 of them are studies in people (0 randomised trials), 2 are reviews, 4 are studies in animals and 22 are studies only in the lab.
The most important ones are listed under Sources.
What this means for you: Results in animals or in cells often do not hold in people. Do not stop or change your medicines because of it. Ask your doctor before you start taking it.
Sources
- Human-Induced Pluripotent Stem Cell-Based Modeling of Cardiac Storage Disorders.2017 · Curr Cardiol Rep · Review
- [Gene therapy of Gaucher's and Fabry's diseases: current status and prospects].2002 · J Soc Biol · Review
- Generation and characterization of induced pluripotent stem cells from a patient with classic Fabry disease.2026 · Intractable Rare Dis Res · In animals
- Usefulness of antibody-drug conjugate as preconditioning for hematopoietic stem cell-targeted gene therapy in wild-type and Fabry disease mouse models.2024 · Mol Genet Metab · In animals
- In Vivo Delivery of Therapeutic Molecules by Transplantation of Genome-Edited Induced Pluripotent Stem Cells.2023 · Cell Transplant · In animals
- Induced pluripotent stem cells derived from mouse models of lysosomal storage disorders.2010 · Proc Natl Acad Sci U S A · In animals
- Generation of two induced pluripotent stem cell lines from Fabry disease patients carrying GLA mutations.2026 · Stem Cell Res · In the lab
- Generation of diseased and isogenic control human induced pluripotent stem cell lines MHHi043-A & MHHi043-B from a female Fabry disease patient carrying c.644A > G missense mutation.2026 · Stem Cell Res · In the lab
- Generation of human induced pluripotent stem cell line MHHi040-A from a female Fabry disease patient carrying c.644A>G missense mutation.2026 · Stem Cell Res · In the lab
- Generation of an induced pluripotent stem cell line (SMBCi022-A) from a patient with Fabry disease.2025 · Stem Cell Res · In the lab
- Generation of a human-induced pluripotent stem cell (hiPSC) line as a cellular model of Fabry disease from a patient carrying the p.A143T variant in the GLA gene (AOUMEYi005-A).2026 · Stem Cell Res · Other paper
- Clinical characteristics and induced pluripotent stem cells (iPSCs) disease model of Fabry disease caused by a novel GLA mutation.2024 · QJM · Other paper
- Generation of the induced pluripotent stem cell line UKWNLi005-A derived from a patient with the GLA mutation c.376A > G of unknown pathogenicity in Fabry disease.2022 · Stem Cell Res · Other paper
- Generation of an induced pluripotent stem cell line (ZJUi007-A) from a 11-year-old patient of Fabry disease.2021 · Stem Cell Res · Other paper