Murdoch Children's Research Institute

Running trials

• Recruiting

  Investigating the Efficacy of a Paediatric Fertility Preservation Decision Aid in Parents and Adolescents and Young Adults (CAYA) Cancer Survivors

  NCT06894810· Murdoch Childrens Research Institute· Source

• Recruiting

  A Clinical Trial of Study Medicine (Marstacimab) in Pediatric Patients With Hemophilia A or Hemophilia B

  NCT05611801· Phase 3· Pfizer· Source

• Active, not recruiting

  A Study to Assess the Safety and Efficacy of Vatiquinone in Participants With Friedreich Ataxia

  NCT05515536· Phase 3· PTC Therapeutics· Source

• Recruiting

  International Multicentric Observational Study to Characterize Subpopulations of Patients With Autism Spectrum Disorder

  NCT05590715· Stalicla SA· Source

• Active, not recruiting

  Safety, Tolerability, Pharmacodynamic, Efficacy, and Pharmacokinetic Study of DYNE-251 in Participants With Duchenne Muscular Dystrophy Amenable to Exon 51 Skipping

  NCT05524883· Phase 1/2· Dyne Therapeutics· Source

• Recruiting

  Generation Victoria Cohort 2020s: A Statewide Longitudinal Cohort Study of Victorian Children and Their Parents

  NCT05394363· Murdoch Childrens Research Institute· Source

• Active, not recruiting

  The PEBBLES Study - Testing a Strategy for Preventing Eczema and Food Allergy in High Risk Infants

  NCT03667651· Phase 3· University of Melbourne· Source

Recruiting at the same time

How many trials recruit for the same indication here at once. A count, not a rating.

• Autism1 recruiting
• Childhood cancers1 recruiting
• Haemophilia1 recruiting
• Obesity1 recruiting

Closed trials

• Terminated

  Extension Study of Pimavanserin in Irritability Associated With Autism Spectrum Disorder

  NCT05555615· Phase 2/3· ACADIA Pharmaceuticals Inc.· Source

• Completed

  Pimavanserin for the Treatment of Irritability Associated With Autism Spectrum Disorder

  NCT05523895· Phase 2/3· ACADIA Pharmaceuticals Inc.· Source

• Recruiting

  Otoferlin Gene-mediated Hearing Loss Natural History Study

  NCT05572073· Akouos, Inc.· Source

• Completed

  Allergic Disease Onset Prevention Study

  NCT05003804· Phase 1/2· Siolta Therapeutics, Inc.· Source

• Completed

  AB-2004 in Treatment of Irritability Associated With Autism Spectrum Disorder (ASD)

  NCT04895215· Phase 2· Vertero Therapeutics· Source

• Terminated

  Phase 3 Trial of Pamrevlumab or Placebo in Combination With Systemic Corticosteroids in Participants With Ambulatory DMD

  NCT04632940· Phase 3· Kyntra Bio· Source

• Completed

  A Research Study to Compare a New Medicine Oral Semaglutide to a Dummy Medicine in Children and Teenagers With Type 2 Diabetes

  NCT04596631· Phase 3· Novo Nordisk A/S· Source

• Completed

  Micronised Resveratrol as a Treatment for Friedreich Ataxia

  NCT03933163· Phase 2· Murdoch Childrens Research Institute· Source

• Completed

  A Study to Evaluate Upadacitinib in Adolescents and Adults With Moderate to Severe Atopic Dermatitis (Measure Up 2)

  NCT03607422· Phase 3· AbbVie· Source

Conditions

Diseases this institution publishes on or runs trials for.

• Epilepsy59 works · 0 trials
• Cerebral palsy36 works · 0 trials
• Autism20 works · 4 trials
• Cystic fibrosis19 works · 0 trials
• Childhood cancers14 works · 1 trial
• Cytomegalovirus infection11 works · 0 trials
• Friedreich ataxia11 works · 2 trials
• Spinal muscular atrophy8 works · 0 trials
• Dystonia6 works · 0 trials