Children's Medical Center

The trials here

What the trial at this site is about, from its registry record.

Conditions

• Spinal muscular atrophy

Running trials

• Not yet recruiting

  SPX-01 Gene Therapy in Pediatric Patients With Spinal Muscular Atrophy Type 1 (RISE)

  NCT07903376· Early phase 1· Exir Gene Pharmed· Source

  Contact: Maryam Bemanalizadeh, MD

Recruiting at the same time

How many trials recruit for the same indication here at once. A count, not a rating.

• Spinal muscular atrophy1 recruiting