Clinic for Special Children

The trials here

What the 2 trials at this site are about, from their registry records.

Conditions

• Spinal muscular atrophy2 trials

Phase

• Phase 32 trials

Status

• Active, not recruiting1 trial
• Completed1 trial

Lead sponsor

• Novartis Gene Therapies1 trial
• Novartis Pharmaceuticals1 trial

Running trials

• Active, not recruiting

  Long-term Follow-up Study of Patients Receiving Onasemnogene Abeparvovec-xioi

  NCT04042025· Phase 3· Novartis Gene Therapies· Source

Closed trials

• Completed

  Efficacy and Safety of Intrathecal OAV101 (AVXS-101) in Pediatric Patients With Type 2 Spinal Muscular Atrophy (SMA)

  NCT05089656· Phase 3· Novartis Pharmaceuticals· Source