Rare Disease Research

The trials here

What the 2 trials at this site are about, from their registry records.

Conditions

• Duchenne muscular dystrophy2 trials

Phase

• Phase 22 trials

Status

• Active, not recruiting2 trials

Lead sponsor

• Avidity Biosciences, Inc.1 trial
• Edgewise Therapeutics, Inc.1 trial

Running trials

• Active, not recruiting

  Phase 2 Study of EDG-5506 in Children and Adolescents With Duchenne Muscular Dystrophy Previously Treated With Gene Therapy

  NCT06100887· Phase 2· Edgewise Therapeutics, Inc.· Source

• Active, not recruiting

  Ph2 Open-label Study of AOC 1044 in Duchenne Muscular Dystrophy Participants With Mutations Amenable to Exon44 Skipping

  NCT06244082· Phase 2· Avidity Biosciences, Inc.· Source