Rare Disease Research NC, LLC

The trials here

What the 2 trials at this site are about, from their registry records.

Conditions

• Duchenne muscular dystrophy1 trial
• Spinal muscular atrophy1 trial

Phase

• Phase 21 trial
• Phase 31 trial

Status

• Active, not recruiting1 trial
• Recruiting1 trial

Lead sponsor

• argenx1 trial
• Capricor Inc.1 trial

Running trials

• Recruiting

  A Study to Assess the Safety, Tolerability, Efficacy, Pharmacokinetics, and Immunogenicity of Intravenous Administration of ARGX-119 in Pediatric Participants Aged 5 to Less Than 18 Years With Spinal Muscular Atrophy

  NCT07287982· Phase 2· argenx· Source

  Contact: Norma Davis

• Active, not recruiting

  A Study of Deramiocel (CAP-1002) in Ambulatory and Non-Ambulatory Patients With Duchenne Muscular Dystrophy

  NCT05126758· Phase 3· Capricor Inc.· Source

Recruiting at the same time

How many trials recruit for the same indication here at once. A count, not a rating.

• Spinal muscular atrophy1 recruiting