Taking people in TaiwanNo phase
Long-term follow-up of people with Pompe disease receiving enzyme replacement therapy
Follows people with Pompe disease who receive enzyme replacement therapy over time.
Plain-language title generated from the registry record
Registry title: A Long-term Study for the Outcome of Pompe Disease
Key facts
- Where
- Taipei, TaiwanSee the site
Where in Taiwan
- National Taiwan University HospitalTaipei, TaiwanTaking people
Questions to ask the study team
- How often do I need to come in, and for how long each time?
- Are travel costs paid?
- Can I keep my own doctor?
- What happens if I want to stop?
Trial details
- Who runs it
- National Taiwan University Hospital
- Trial code
- NCT02399748
- Record updated
- 18 July 2017
- Original description
Prospectively follow patients with Pompe disease underwent enzyme replacement therapy.Read full original descriptionShow less
A Long-term Study for the Outcome of Pompe Disease
Prospectively follow patients with Pompe disease underwent enzyme replacement therapy.
Inclusion: Confirm diagnosis with Pompe disease, is or is preparing receiving enzyme replacement therapy.
Exclusion: No.