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NCT04794101Active, not recruitingPhase 3

Follow-up Gene Therapy Trial for the Treatment of X-linked Retinitis Pigmentosa Associated With Variants in the RPGR Gene

Phase 3 Follow-up Study of AAV5-hRKp.RPGR for the Treatment of X-linked Retinitis Pigmentosa Associated With Variants in the RPGR Gene

Source: ClinicalTrials.gov · Last updated 25 Sept 2026

Brief summary (registry, in English)

A clinical trial of AAV5-hRKp.RPGR vector for participants with X-linked retinitis pigmentosa (XLRP)

Status (registry)
Active, not recruiting
Phase (registry)
Phase 3
Study type
Interventional
Enrollment
97 (actual)
First submitted
15 Dec 2020
Start date
4 Dec 2020
Primary completion date
20 Sept 2029
Lead sponsor
MeiraGTx Ocular UK Ltd
NCT number
NCT04794101
EU CT number
2024-511411-25-00
EudraCT number
2020-002255-37

What you commit to

  • Study type: Interventional · Phase 3
  • Participants enrolled: 97
  • From 4 Dec 2020 to the primary completion date, 20 Sept 2029
  • 26 sites in 11 countries
  • Visits and tests: ask the trial team, the registry does not list them

Built from the registry fields of ClinicalTrials.gov. It describes the study, not your situation.

Who cannot take part

Copied verbatim from ClinicalTrials.gov and grouped by topic. Only the trial team decides who can take part.

Other

  • None

Who the study is looking for

  • Male or female, 3 years of age or older, has XLRP confirmed by a retinal specialist and has a predicted disease-causing sequence variant in RPGR confirmed by an accredited laboratory.

Age in the registry: 3 years to 64 years · Sex: All · Does not accept healthy volunteers

Full criteria on ClinicalTrials.gov

Sites (26)

Sites in registry order. Pick your city on the disease page to sort them by distance.

SiteCityCountrySite status
Universitair Ziekenhuis Gent
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GentBelgiumActive, not recruiting
Hospital for Sick Children
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TorontoCanadaUnknown status
University Hospital Basel, Eye Clinic/Institute of Molecular and Clinical
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BaselSwitzerlandUnknown status
Universite de Lausanne, Hopital ophtalmique Jules-Gonin
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LausanneSwitzerlandUnknown status
Rigshospitalet
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GlostrupDenmarkActive, not recruiting
Hospital Universitario Fundación Jiménez Díaz
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MadridSpainActive, not recruiting
Quinze-Vingts National Ophthalmology Hospital
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ParisFranceActive, not recruiting
NHS Lothian
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EdinburghUnited KingdomUnknown status
Gartnavel General Hospital
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GlasgowUnited KingdomUnknown status
St James University Hospital
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LeedsUnited KingdomUnknown status
Moorfields Eye Hospital
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LondonUnited KingdomUnknown status
Hadassah medical Center
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JerusalemIsraelUnknown status
Careggi University Hospital
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FlorenceItalyActive, not recruiting
Azienda Ospedaliera Universitaria - Universita degli Studi della Campania Luigi Vanvitelli
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NaplesItalyActive, not recruiting
Stichting Amsterdam UMC
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AmsterdamNetherlandsActive, not recruiting
Stichting Radboud Universitair Medisch Centrum
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NijmegenNetherlandsActive, not recruiting
Univ of Michigan Medical Center
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Ann ArborUnited StatesUnknown status
Emory University
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AtlantaUnited StatesUnknown status
Retina Consultants of Houston
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BellaireUnited StatesUnknown status
Massachusetts Eye and Ear Infirmary
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BostonUnited StatesUnknown status
Duke Eye Center
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DurhamUnited StatesUnknown status
VitreoRetinal Associates, PA
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GainesvilleUnited StatesUnknown status
Shiley Eye Institute Jacobs Retina Center
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La JollaUnited StatesUnknown status
Childrens Hospital Los Angeles
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Los AngelesUnited StatesUnknown status
Stanford Health Care
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Palo AltoUnited StatesUnknown status
University of Pittsburgh Medical Center (UPMC)
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PittsburghUnited StatesUnknown status

This page is information, not medical advice. Discuss any trial with your doctor.