NCT04794101Active, not recruitingPhase 3
Follow-up Gene Therapy Trial for the Treatment of X-linked Retinitis Pigmentosa Associated With Variants in the RPGR Gene
Phase 3 Follow-up Study of AAV5-hRKp.RPGR for the Treatment of X-linked Retinitis Pigmentosa Associated With Variants in the RPGR Gene
Source: ClinicalTrials.gov · Last updated 25 Sept 2026
Brief summary (registry, in English)
A clinical trial of AAV5-hRKp.RPGR vector for participants with X-linked retinitis pigmentosa (XLRP)
- Status (registry)
- Active, not recruiting
- Phase (registry)
- Phase 3
- Study type
- Interventional
- Enrollment
- 97 (actual)
- First submitted
- 15 Dec 2020
- Start date
- 4 Dec 2020
- Primary completion date
- 20 Sept 2029
- Lead sponsor
- MeiraGTx Ocular UK Ltd
- Diseases
- Retinitis pigmentosa
- NCT number
- NCT04794101
- EU CT number
- 2024-511411-25-00
- EudraCT number
- 2020-002255-37
What you commit to
- Study type: Interventional · Phase 3
- Participants enrolled: 97
- From 4 Dec 2020 to the primary completion date, 20 Sept 2029
- 26 sites in 11 countries
- Visits and tests: ask the trial team, the registry does not list them
Built from the registry fields of ClinicalTrials.gov. It describes the study, not your situation.
Who cannot take part
Copied verbatim from ClinicalTrials.gov and grouped by topic. Only the trial team decides who can take part.
Other
- None
Who the study is looking for
- Male or female, 3 years of age or older, has XLRP confirmed by a retinal specialist and has a predicted disease-causing sequence variant in RPGR confirmed by an accredited laboratory.
Age in the registry: 3 years to 64 years · Sex: All · Does not accept healthy volunteers
Sites (26)
Sites in registry order. Save your city in your profile to sort them by distance.
| Site | City | Country | Site status |
|---|---|---|---|
| Universitair Ziekenhuis Gent Coordinator of this site? Confirm its status | Gent | Belgium | Active, not recruiting |
| Hospital for Sick Children Coordinator of this site? Confirm its status | Toronto | Canada | Unknown status |
| University Hospital Basel, Eye Clinic/Institute of Molecular and Clinical Coordinator of this site? Confirm its status | Basel | Switzerland | Unknown status |
| Universite de Lausanne, Hopital ophtalmique Jules-Gonin Coordinator of this site? Confirm its status | Lausanne | Switzerland | Unknown status |
| Rigshospitalet Coordinator of this site? Confirm its status | Glostrup | Denmark | Active, not recruiting |
| Hospital Universitario Fundación Jiménez Díaz Coordinator of this site? Confirm its status | Madrid | Spain | Active, not recruiting |
| Quinze-Vingts National Ophthalmology Hospital Coordinator of this site? Confirm its status | Paris | France | Active, not recruiting |
| NHS Lothian Coordinator of this site? Confirm its status | Edinburgh | United Kingdom | Unknown status |
| Gartnavel General Hospital Coordinator of this site? Confirm its status | Glasgow | United Kingdom | Unknown status |
| St James University Hospital Coordinator of this site? Confirm its status | Leeds | United Kingdom | Unknown status |
| Moorfields Eye Hospital Coordinator of this site? Confirm its status | London | United Kingdom | Unknown status |
| Hadassah medical Center Coordinator of this site? Confirm its status | Jerusalem | Israel | Unknown status |
| Careggi University Hospital Coordinator of this site? Confirm its status | Florence | Italy | Active, not recruiting |
| Azienda Ospedaliera Universitaria - Universita degli Studi della Campania Luigi Vanvitelli Coordinator of this site? Confirm its status | Naples | Italy | Active, not recruiting |
| Stichting Amsterdam UMC Coordinator of this site? Confirm its status | Amsterdam | Netherlands | Active, not recruiting |
| Stichting Radboud Universitair Medisch Centrum Coordinator of this site? Confirm its status | Nijmegen | Netherlands | Active, not recruiting |
| Univ of Michigan Medical Center Coordinator of this site? Confirm its status | Ann Arbor | United States | Unknown status |
| Emory University Coordinator of this site? Confirm its status | Atlanta | United States | Unknown status |
| Retina Consultants of Houston Coordinator of this site? Confirm its status | Bellaire | United States | Unknown status |
| Massachusetts Eye and Ear Infirmary Coordinator of this site? Confirm its status | Boston | United States | Unknown status |
| Duke Eye Center Coordinator of this site? Confirm its status | Durham | United States | Unknown status |
| VitreoRetinal Associates, PA Coordinator of this site? Confirm its status | Gainesville | United States | Unknown status |
| Shiley Eye Institute Jacobs Retina Center Coordinator of this site? Confirm its status | La Jolla | United States | Unknown status |
| Childrens Hospital Los Angeles Coordinator of this site? Confirm its status | Los Angeles | United States | Unknown status |
| Stanford Health Care Coordinator of this site? Confirm its status | Palo Alto | United States | Unknown status |
| University of Pittsburgh Medical Center (UPMC) Coordinator of this site? Confirm its status | Pittsburgh | United States | Unknown status |
This page is information, not medical advice. Discuss any trial with your doctor.