NCT05874310RecruitingEarly phase 1
Gene Therapy for Subjects With RPGR Mutation-associated X-linked Retinitis Pigmentosa
An Open-label, Single-center, Dose-escalation Clinical Study to Evaluate the Safety, Tolerability, and Preliminary Efficacy of Intraocular Administration of FT-002 in Subjects With RPGR Mutation-associated X-linked Retinitis Pigmentosa.
Source: ClinicalTrials.gov · Last updated 24 May 2023 · Not updated for over 12 months - ask the site whether it is still open
Brief summary (registry, in English)
A clinical trial of gene therapy for patients with X-linked retinitis pigmentosa (XLRP).
- Status (registry)
- Recruiting
- Phase (registry)
- Early phase 1
- Study type
- Interventional
- Enrollment
- 18 (estimated)
- First submitted
- 29 Apr 2023
- Start date
- 1 Feb 2023
- Primary completion date
- 31 Oct 2023
- Lead sponsor
- Frontera Therapeutics
- Diseases
- Retinitis pigmentosa
- NCT number
- NCT05874310
What you commit to
- Study type: Interventional · Early phase 1
- Planned participants: 18
- From 1 Feb 2023 to the primary completion date, 31 Oct 2023
- 2 sites in 1 country
- Visits and tests: ask the trial team, the registry does not list them
Built from the registry fields of ClinicalTrials.gov. It describes the study, not your situation.
Who cannot take part
Copied verbatim from ClinicalTrials.gov and grouped by topic. Only the trial team decides who can take part.
Prior treatment
- 1.Have other retinal degenerative diseases, such as retinal degeneration caused by other known Inherited retinal disease gene variants or previously received an gene therapy product.
Who the study is looking for
- 1.Subjects that are willing and able to follow study procedures; 2.Males aged 8-45 years old at the time of signing the Informed Consent Form; 4.Subjects who are confirmed with variants of RPGR ;
Age in the registry: 8 years to 45 years · Sex: Male · Does not accept healthy volunteers
Sites (2)
Sites in registry order. Pick your city on the disease page to sort them by distance.
| Site | City | Country | Site status |
|---|---|---|---|
| Peking Union Medical College Hospital Coordinator of this site? Confirm its status | Beijing | China | Recruiting |
| Eye ENT Hospital of Fudan University Coordinator of this site? Confirm its status | Shanghai | China | Recruiting |
This page is information, not medical advice. Discuss any trial with your doctor.