Duchenne muscular dystrophy: open trials in Belgium

19 open trials have a site in Belgium. Registry data; only the trial team decides who can take part.

2023-504520-26-00
Study in which all the patients take the same investigational drug with the aim of evaluate the long-term safety, tolerability, and efficacy of GIVINOSTAT in all the patients affected with Duchenne Muscolar Dystrophy who have been already treated in one of the GIVINOSTAT studies in the past
Trial Treatment · Phase 3 · Italfarmaco S.p.A.
UZ Leuven, Leuven · Centre Hospitalier Regional de la Citadelle, Liège
Registry updated 2026-11-06
NCT07587242
A Phase 3 Study to Evaluate the Safety and Efficacy of AOC 1044 (Also Referred to as Delpacibart Zotadirsen) in Participants With DMD With Gene Mutations Amenable to Exon 44 Skipping
Trial Treatment · Phase 3 · Avidity Biosciences, Inc.
UZ Leuven, Leuven · Centre Hospitalier Regional de la Citadelle, Liège
Registry updated 2026-10-13
NCT07856329
A Clinical Study to Assess Safety, Efficacy and Pharmacodynamic Profile of GNT0004 in Duchenne Muscular Dystrophy
Trial Treatment · Phase 2/3 · Genethon
Association Hospitaliere De Bruxelles Hopital Universitaire Des Enfants Reine Fabiola, Brussels · UZ Leuven, Leuven · Centre Hospitalier Regional de la Citadelle, Liège
Registry updated 2026-10-13
2024-511823-32-00
A Phase 2 Open-label (Core Phase Plus Extension Phase) With 2 Cohorts Study to Assess the Pharmacokinetics and Safety of Givinostat in DMD Patients Ages From at Least 2 Years to Less Than 6 Years Old
Trial Treatment · Phase 2 · Italfarmaco S.p.A.
Association Hospitaliere De Bruxelles Hopital Universitaire Des Enfants Reine Fabiola, Brussels
Registry updated 2026-10-09
NCT07160634
A Study of SGT-003 Gene Therapy in Ambulant Males With Duchenne Muscular Dystrophy (IMPACT DUCHENNE)
Trial Treatment · Phase 3 · Solid Biosciences Inc.
Association Hospitaliere De Bruxelles Hopital Universitaire Des Enfants Reine Fabiola, Brussels · UZ Leuven, Leuven
Registry updated 2026-09-28
NCT06066580
Open-Label Extension of EDG-5506 in Participants With Becker Muscular Dystrophy
Trial Treatment · Phase 2 · Edgewise Therapeutics, Inc.
University Hospital Gent, Ghent · Universitaire Ziekenhuizen Leuven, Leuven · Centre Hospitalier Regional de la Citadelle, Liège
Registry updated 2026-09-17
NCT07037862
A Study in Participants With Duchenne Muscular Dystrophy Amenable to Exon 44 Skipping to Evaluate the Safety and Efficacy of ENTR-601-44
Trial Treatment · Phase 1/2 · Entrada Therapeutics, Inc.
Universitair Ziekenhuis Gent, Gent · UZ Leuven, Leuven · Centre Hospitalier Regional de la Citadelle, Liège
Registry updated 2026-08-13
NCT07038824
A Study in Participants With Duchenne Muscular Dystrophy Amenable to Exon 45 Skipping to Evaluate the Safety and Efficacy of ENTR-601-45
Trial Treatment · Phase 1/2 · Entrada Therapeutics, Inc.
Universitair Ziekenhuis Gent, Gent · UZ Leuven, Leuven · Centre Hospitalier Regional de la Citadelle, Liège
Registry updated 2026-08-13
NCT05933057
Efficacy, Safety and Tolerability of Givinostat in Non-ambulant Patients With Duchenne Muscular Dystrophy
Trial Treatment · Phase 3 · Italfarmaco
UZ Leuven, Leuven
Registry updated 2026-07-24
NCT07682129
Long-Term Extension Study in Participants With Duchenne Muscular Dystrophy Amenable to Exon Skipping to Evaluate the Safety and Efficacy of Endosomal Escape Vehicle Phosphorodiamidate Morpholino Oligomer Platform Products (ELEVATE-LTE)
Trial Treatment · Phase 2 · Entrada Therapeutics, Inc.
Universitair Ziekenhuis Gent, Gent · UZ Leuven, Leuven · Centre Hospitalier Regional de la Citadelle, Liège
Registry updated 2026-07-02
NCT07664124
Digital Monitoring of Upper Limb Function in Non-Ambulant DMD
Trial Treatment · Centre Hospitalier Universitaire de Liege
Centre de référence des maladies neuromusculaire, Centre Hospitalier Régional de la Citadelle, Liège
Registry updated 2026-06-23
2025-523087-20-00
A Phase 3, Randomized, Double-Blind, Placebo-Controlled, Global Study with an Open-Label Extension to Evaluate the Efficacy and Safety of Intravenous AOC 1044 (delpacibart zotadirsen) for the Treatment of DMD with Gene Mutations Amenable to Exon 44 Skipping
Trial Treatment · Phase 3 · Avidity Biosciences Inc.
UZ Leuven, Leuven · Centre Hospitalier Regional de la Citadelle, Liège
Registry updated 2026-05-27
NCT03882827
Natural History of Duchenne Muscular Dystrophy
Research · Genethon
Centre Hospitalier Universitaire Brugmann, Brussels · UZ Leuven, Leuven · CHR Hôpital de la Citadelle, Liège
Registry updated 2026-02-12
NCT05967351
A Long-term Follow-up Study of Participants Who Received Delandistrogene Moxeparvovec (SRP-9001) in a Previous Clinical Study
Trial Treatment · Phase 3 · Sarepta Therapeutics, Inc.
Universitair Ziekenhuis Gent, Gent
Registry updated 2026-02-06
NCT03373968
Givinostat in Duchenne's Muscular Dystrophy Long-term Safety and Tolerability Study
Trial Treatment · Phase 2/3 · Italfarmaco
University Hospitals Leuven, Neuromuscular Reference Centre, Child Neurology, Leuven · Hospital de La Citadelle, Centre de Référence des Maladies Neuromuscolaires (CRMN), Liège
Registry updated 2026-01-21
NCT07286565
Active NBS Study: Decentralised Monitoring Motor Development in Children With Duchenne Muscular Dystrophy or Spinal Muscular Atrophy Identified by Newborn Screening
Trial Treatment · Centre Hospitalier Universitaire de Liege
Centre de référence des maladies neuromusculaire, Centre Hospitalier Régional de la Citadelle, Liège
Registry updated 2025-12-16
NCT06769633
Pharmacokinetics and Safety of Givinostat in DMD Patients Ages From at Least 2 Years to Less Then 6 Years Old
Trial Treatment · Phase 2 · Italfarmaco
Queen Fabiola Children's University Hospital HUDERF, Brussels
Registry updated 2025-07-10
NCT05982119
Assessments in Patients With Muscular Pathology and in Control Subjects : The ActiLiège Next Study
Trial Treatment · Centre Hospitalier Universitaire de Liege
CHR de la Citadelle, Liège
Registry updated 2025-05-20
NCT06773988
Follow-up of NIV At Home in Patients with Duchenne Muscular Dystrophy
Research · Universitaire Ziekenhuizen KU Leuven
Universitaire Ziekenhuizen KU Leuven, Leuven
Registry updated 2025-01-14

All Duchenne muscular dystrophy trials and the map

This page is not medical advice. Talk to your doctor before contacting a trial.

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