Duchenne muscular dystrophy trials in United States

In United States 36 Also abroad 87

36 trials · From ClinicalTrials.gov, checked 11 November 2026. Ask the study team whether a trial fits you.

No phaseTaking people
Urinary Titin Biomarker in DMD
Where
Philadelphia
Age
2 years to 10 years
People
50
Run by
Children's Hospital of Philadelphia
See details and how to joinNCT07332013
No phaseEnrolling by invitation
Long Term Follow-up for RGX-202
Where
Chicago, Dallas, Little Rock, Palo Alto, Richmond
People
66
Run by
REGENXBIO Inc.
See details and how to joinNCT06491927
Phase 1Taking people
Trial of Cell Based Therapy for DMD
Where
Minneapolis
Age
18 years and over
People
8
Run by
Masonic Cancer Center, University of Minnesota
See details and how to joinNCT06692426
Phase 3Enrolling by invitation
A Long-term Follow-up Study of Participants Who Received Delandistrogene Moxeparvovec (SRP-9001) in a Previous Clinical Study
Where
Aurora, Baltimore, Boston, Chicago, Columbus, Dallas, Durham, Gainesville, Iowa City, Little Rock, Los Angeles, Milwaukee, New York, Norfolk, Palo Alto, Philadelphia, Portland, Rochester, Sacramento, Salt Lake City, San Diego, St Louis
Age
Up to 64 years
People
400 worldwide
Run by
Sarepta Therapeutics, Inc.
See details and how to joinNCT05967351 · EU 2023-505043-39-00
Phase 2/3Taking people
Givinostat in Duchenne's Muscular Dystrophy Long-term Safety and Tolerability Study
Where
Atlanta, Gainesville, Hartford, Iowa City, Philadelphia, Portland, Richmond, Sacramento, San Diego, St Louis
Age
7 years and over
People
206 worldwide
Run by
Italfarmaco
See details and how to joinNCT03373968
No phaseEnrolling by invitation
Derivation of Human Induced Pluripotent Stem (iPS) Cells to Heritable Cardiac Arrhythmias
Where
Baltimore
Age
18 years to 85 years
People
100
Run by
Johns Hopkins University
See details and how to joinNCT02413450
No phaseTaking people
Wearable Technology to Evaluate Hyperglycemia and HRV in DMD - Longitudinal Aim
Where
Nashville
Age
10 years and over
People
10
Run by
Vanderbilt University Medical Center
See details and how to joinNCT06093100
No phaseTaking people
Magnetic Resonance Imaging and Biomarkers for Muscular Dystrophy
Where
Gainesville, Philadelphia, Portland
Age
5 years to 62 years
People
550
Run by
University of Florida
See details and how to joinNCT01484678
No phaseTaking people
DMD Voice: Qualitative Interviews With Patients and Caregivers
Where
Yardley
Age
10 years and over
People
68
Run by
Red Nucleus Enterprise Solutions, LLC
See details and how to joinNCT06925269
Phase 1Taking people
Modulation of SERCA2a of Intra-Myocytic Calcium Trafficking in Cardiomyopathy Secondary to Duchenne Muscular Dystrophy
Where
Cincinnati, Columbus, Kansas City
Age
18 years and over
People
12
Run by
Sardocor Corp.
See details and how to joinNCT06224660
No phaseTaking people
Molecular Analysis of Patients With Neuromuscular Disease
Where
Boston
Age
1 week to 100 years
People
1,000
Run by
Boston Children's Hospital
See details and how to joinNCT00390104