Mitochondrial disease trials in United States

28 trials · From ClinicalTrials.gov, checked 15 November 2026. Ask the study team whether a trial fits you.

• No phaseEnrolling by invitation
  Tissue Sample Study for Mitochondrial Disorders

  Where

  New York

  People

  6,900

  Run by

  Columbia University

  See details and how to joinNCT01803906
• Phase 1Taking people
  Applying pGz in Mitochondrial Disease

  Where

  Philadelphia

  Age

  10 years to 60 years

  People

  90

  Run by

  Children's Hospital of Philadelphia

  See details and how to joinNCT05569122
• No phaseTaking people
  The International Registry for Leigh Syndrome

  Where

  Houston

  Age

  0 days to 100 years

  People

  200

  Run by

  The University of Texas Health Science Center, Houston

  See details and how to joinNCT03137355