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Neuroblastoma: open trials in United States

59 open trials have a site in United States. Registry data; only the trial team decides who can take part.

  • NCT01005654

    Prospective Comprehensive Molecular Analysis of Endocrine Neoplasms

    Research · National Cancer Institute (NCI)

    National Institutes of Health Clinical Center, Bethesda

    Registry updated 2026-11-05

  • NCT06176989

    Enasidenib in IDH2-Mutated Malignant Sinonasal and Skull Base Tumors

    Trial Treatment · Phase 2 · National Cancer Institute (NCI)

    National Institutes of Health Clinical Center, Bethesda

    Registry updated 2026-11-05

  • NCT04837547

    PEACH TRIAL- Precision Medicine and Adoptive Cellular Therapy

    Trial Treatment · Phase 1 · University of Florida

    Levine Children's Hospital, Charlotte · University of Florida, Gainesville · Penn State Milton S. Hershey Medical Center and Children's Hospital, Hershey

    Registry updated 2026-11-04

  • NCT07437963

    Testing the Addition of Iberdomide to Therapy in People With Neuroblastoma That Has Come Back, Not Responded to Treatment, or Gotten Worse

    Trial Treatment · Phase 1/2 · National Cancer Institute (NCI)

    Lurie Children's Hospital-Chicago, Chicago · Memorial Sloan-Kettering Cancer Center, New York · Children's Oncology Group, Oakland

    Registry updated 2026-11-04

  • NCT07549321

    A Safety and Efficacy Study of hu14 in High-Risk Neuroblastoma Patients

    Trial Treatment · Phase 2/3 · Renaissance Pharma Ltd.

    Children's Hospital Colorado Anschutz Medical, Aurora · The University Of Chicago, Chicago · University of Texas, Southwestern, Dallas · Duke University Medical Center, Durham · University of Minnesota/Masonic Children's Hospital, Minneapolis · Children's Hospital of Philadelphia, Philadelphia · University of California, San Francisco (UCSF), San Francisco · The Children's Hospital at Montefiore, The Bronx

    Registry updated 2026-11-03

  • NCT06041516

    A First-in-Human Phase I Trial With Antibody Drug Conjugate ADCT-701 in Neuroendocrine Tumors, Carcinomas and Malignant Peripheral Nerve Sheath Tumors

    Trial Treatment · Phase 1 · National Cancer Institute (NCI)

    National Institutes of Health Clinical Center, Bethesda

    Registry updated 2026-11-02

  • NCT06172296

    Dinutuximab With Chemotherapy, Surgery and Stem Cell Transplantation for the Treatment of Children With Newly Diagnosed High Risk Neuroblastoma

    Trial Treatment · Phase 3 · National Cancer Institute (NCI)

    Children's Hospital Medical Center of Akron, Akron · Albany Medical Center, Albany · University of New Mexico Cancer Center, Albuquerque · Lehigh Valley Hospital-Cedar Crest, Allentown · C S Mott Children's Hospital, Ann Arbor · Mission Hospital, Asheville · Children's Healthcare of Atlanta - Arthur M Blank Hospital, Atlanta · Children's Hospital Colorado, Aurora · Dell Children's Medical Center of Central Texas, Austin · University of Maryland/Greenebaum Cancer Center, Baltimore · Sinai Hospital of Baltimore, Baltimore · Johns Hopkins University/Sidney Kimmel Cancer Center, Baltimore · Eastern Maine Medical Center, Bangor · Walter Reed National Military Medical Center, Bethesda · Children's Hospital of Alabama, Birmingham · Dana-Farber Cancer Institute, Boston · Massachusetts General Hospital Cancer Center, Boston · Roswell Park Cancer Institute, Buffalo · University of Vermont and State Agricultural College, Burlington · UNC Lineberger Comprehensive Cancer Center, Chapel Hill · Medical University of South Carolina, Charleston · Carolinas Medical Center/Levine Cancer Institute, Charlotte · Novant Health Presbyterian Medical Center, Charlotte · University of Virginia Cancer Center, Charlottesville · University of Illinois, Chicago · Lurie Children's Hospital-Chicago, Chicago · University of Chicago Comprehensive Cancer Center, Chicago · Cincinnati Children's Hospital Medical Center, Cincinnati · Cleveland Clinic Foundation, Cleveland · Rainbow Babies and Childrens Hospital, Cleveland · Prisma Health Richland Hospital, Columbia · University of Missouri Children's Hospital, Columbia · Nationwide Children's Hospital, Columbus · Driscoll Children's Hospital, Corpus Christi · UT Southwestern/Simmons Cancer Center-Dallas, Dallas · Medical City Dallas Hospital, Dallas · Geisinger Medical Center, Danville · Dayton Children's Hospital, Dayton · Blank Children's Hospital, Des Moines · Children's Hospital of Michigan, Detroit · Kaiser Permanente Downey Medical Center, Downey · City of Hope Comprehensive Cancer Center, Duarte · Duke University Medical Center, Durham · El Paso Children's Hospital, El Paso · Sanford Broadway Medical Center, Fargo · Broward Health Medical Center, Fort Lauderdale · Golisano Children's Hospital of Southwest Florida, Fort Myers · Cook Children's Medical Center, Fort Worth · UF Health Cancer Institute - Gainesville, Gainesville · Corewell Health Grand Rapids Hospitals - Helen DeVos Children's Hospital, Grand Rapids · Saint Vincent Hospital Cancer Center Green Bay, Green Bay · East Carolina University, Greenville · BI-LO Charities Children's Cancer Center, Greenville · Hackensack University Medical Center, Hackensack · Connecticut Children's Medical Center, Hartford · Memorial Regional Hospital/Joe DiMaggio Children's Hospital, Hollywood · Kapiolani Medical Center for Women and Children, Honolulu · UT MD Anderson Cancer Center, Houston · Baylor College of Medicine/Dan L Duncan Comprehensive Cancer Center, Houston · Edwards Comprehensive Cancer Center, Huntington · Ascension Saint Vincent Indianapolis Hospital, Indianapolis · Riley Hospital for Children, Indianapolis · University of Iowa/Holden Comprehensive Cancer Center, Iowa City · University of Mississippi Medical Center, Jackson · Nemours Children's Clinic-Jacksonville, Jacksonville · Bronson Methodist Hospital, Kalamazoo · Children's Mercy Hospitals and Clinics, Kansas City · East Tennessee Childrens Hospital, Knoxville · Alliance for Childhood Diseases/Cure 4 the Kids Foundation, Las Vegas · Dartmouth Hitchcock Medical Center/Dartmouth Cancer Center, Lebanon · University of Kentucky/Markey Cancer Center, Lexington · Arkansas Children's Hospital, Little Rock · Loma Linda University Medical Center, Loma Linda · Miller Children's and Women's Hospital Long Beach, Long Beach · Cedars-Sinai Medical Center, Los Angeles · Mattel Children's Hospital UCLA, Los Angeles · Children's Hospital Los Angeles, Los Angeles · Norton Children's Hospital, Louisville · UMC Cancer Center / UMC Health System, Lubbock · Covenant Children's Hospital, Lubbock · Valley Children's Hospital, Madera · University of Wisconsin Carbone Cancer Center - University Hospital, Madison · Marshfield Medical Center-Marshfield, Marshfield · Saint Jude Children's Research Hospital, Memphis · Banner Children's at Desert, Mesa · Nicklaus Children's Hospital, Miami · University of Miami Miller School of Medicine-Sylvester Cancer Center, Miami · Children's Hospital of Wisconsin, Milwaukee · NYU Langone Hospital - Long Island, Mineola · University of Minnesota/Masonic Cancer Center, Minneapolis · Children's Hospitals and Clinics of Minnesota - Minneapolis, Minneapolis · USA Health Strada Patient Care Center, Mobile · West Virginia University Healthcare, Morgantown · Morristown Medical Center, Morristown · The Children's Hospital at TriStar Centennial, Nashville · Vanderbilt University/Ingram Cancer Center, Nashville · Newark Beth Israel Medical Center, Newark · Saint Peter's University Hospital, New Brunswick · Rutgers Cancer Institute of New Jersey-Robert Wood Johnson University Hospital, New Brunswick · Yale University, New Haven · The Steven and Alexandra Cohen Children's Medical Center of New York, New Hyde Park · Children's Hospital New Orleans, New Orleans · NYP/Columbia University Medical Center/Herbert Irving Comprehensive Cancer Center, New York · Laura and Isaac Perlmutter Cancer Center at NYU Langone, New York · UCSF Benioff Children's Hospital Oakland, Oakland · Kaiser Permanente-Oakland, Oakland · Advocate Children's Hospital-Oak Lawn, Oak Lawn · University of Oklahoma Health Sciences Center, Oklahoma City · University of Nebraska Medical Center, Omaha · Children's Hospital and Medical Center of Omaha, Omaha · Children's Hospital of Orange County, Orange · AdventHealth Orlando, Orlando · Arnold Palmer Hospital for Children, Orlando · Nemours Children's Hospital, Orlando · Lucile Packard Children's Hospital Stanford University, Palo Alto · Advocate Children's Hospital-Park Ridge, Park Ridge · Saint Joseph's Regional Medical Center, Paterson · OSF Children's Hospital of Illinois, Peoria · Children's Hospital of Philadelphia, Philadelphia · Saint Christopher's Hospital for Children, Philadelphia · Phoenix Childrens Hospital, Phoenix · Children's Hospital of Pittsburgh of UPMC, Pittsburgh · Legacy Emanuel Children's Hospital, Portland · Oregon Health and Science University, Portland · Naval Medical Center - Portsmouth, Portsmouth · Rhode Island Hospital, Providence · University of Rochester, Rochester · Mayo Clinic in Rochester, Rochester · Corewell Health Children's, Royal Oak · University of California Davis Comprehensive Cancer Center, Sacramento · Sutter Medical Center Sacramento, Sacramento · Primary Children's Hospital, Salt Lake City · University of Texas Health Science Center at San Antonio, San Antonio · Methodist Children's Hospital of South Texas, San Antonio · Children's Hospital of San Antonio, San Antonio · Rady Children's Hospital - San Diego, San Diego · UCSF Medical Center-Mission Bay, San Francisco · Memorial Health University Medical Center, Savannah · Maine Children's Cancer Program, Scarborough · Seattle Children's Hospital, Seattle · Sanford USD Medical Center - Sioux Falls, Sioux Falls · Providence Sacred Heart Medical Center and Children's Hospital, Spokane · Southern Illinois University School of Medicine, Springfield · Mercy Hospital Saint Louis, St Louis · Washington University School of Medicine, St Louis · Johns Hopkins All Children's Hospital, St. Petersburg · State University of New York Upstate Medical University, Syracuse · Mary Bridge Children's Hospital and Health Center, Tacoma · Montefiore Medical Center - Moses Campus, The Bronx · ProMedica Toledo Hospital/Russell J Ebeid Children's Hospital, Toledo · Banner University Medical Center - Tucson, Tucson · Saint Francis Children's Hospital, Tulsa · New York Medical College, Valhalla · Children's National Medical Center, Washington D.C. · Saint Mary's Medical Center, West Palm Beach · Wesley Medical Center, Wichita · Alfred I duPont Hospital for Children, Wilmington · Wake Forest University Health Sciences, Winston-Salem

    Registry updated 2026-10-30

  • NCT06395103

    Substudy 01A: Zilovertamab Vedotin in Pediatric and Young Adult Participants With Hematologic Malignancies or Solid Tumors (MK-9999-01A/LIGHTBEAM-U01)

    Trial Treatment · Phase 1/2 · Merck Sharp & Dohme LLC

    Children's Hospital Colorado-Center for Cancer and Blood Disorders ( Site 1016), Aurora · Dana-Farber Cancer Institute ( Site 1013), Boston · Sanford Fargo Medical Center-Roger Maris Cancer Center ( Site 1003), Fargo · Corewell Health ( Site 1001), Grand Rapids · University of Texas MD Anderson Cancer Center ( Site 1007), Houston · University of Iowa Health Care. ( Site 1017), Iowa City · Children's Mercy Hospital ( Site 1024), Kansas City · Children's Hospital Los Angeles ( Site 1006), Los Angeles · Rutgers Cancer Institute of New Jersey ( Site 1008), New Brunswick · Yale New Haven Hospital ( Site 1012), New Haven · Memorial Sloan Kettering Cancer Center ( Site 1010), New York · Children's Hospital of Philadelphia (CHOP) ( Site 1021), Philadelphia · Oregon Health and Science University ( Site 1004), Portland · Intermountain - Primary Children's Hospital ( Site 1014), Salt Lake City · Sanford Children's Hospital-Sanford Children's Specialty Clinic ( Site 1015), Sioux Falls · Johns Hopkins All Children's Hospital ( Site 1025), St. Petersburg · New York Medical College ( Site 1023), Valhalla

    Registry updated 2026-10-30

  • NCT02508038

    Alpha/Beta CD19+ Depleted Haploidentical Transplantation + Zometa for Pediatric Hematologic Malignancies and Solid Tumors

    Trial Treatment · Phase 1 · University of Wisconsin, Madison

    University of Wisconsin Carbone Cancer Center, Madison

    Registry updated 2026-10-27

  • NCT02605421

    Myeloablative Consolidation Therapy and Tandem Autologous Stem Cell Rescue in Patients With High-Risk Neuroblastoma

    Trial Treatment · Phase 2 · Masonic Cancer Center, University of Minnesota

    Masonic Cancer Center, University of Minnesota, Minneapolis

    Registry updated 2026-10-27

  • NCT03382158

    International PPB/DICER1 Registry

    Research · Children's Hospitals and Clinics of Minnesota

    Children's Minnesota, Minneapolis

    Registry updated 2026-10-26

  • NCT06995872

    Phase I Trial of rhIL-15 Plus Dinutuximab Plus Irinotecan/Temozolomide for Children and Young Adults With Relapsed/Refractory Neuroblastoma

    Trial Treatment · Phase 1 · National Cancer Institute (NCI)

    National Institutes of Health Clinical Center, Bethesda

    Registry updated 2026-10-21

  • NCT01109394

    Comprehensive Omics Analysis of Pediatric and Adult Solid Tumors and Establishment of a Repository for Related Biological Studies

    Research · National Cancer Institute (NCI)

    National Institutes of Health Clinical Center, Bethesda · Carolinas Medical Center/ Levine Children's Hospital, Charlotte · Tisch Cancer Institute, Mount Sinai Medical Center, New York · Children's Hospital of Orange County (CHOC Children's), Orange · Children's National Medical Center, Washington D.C.

    Registry updated 2026-10-16

  • NCT04755205

    A Natural History Study of Children and Adults With Olfactory Neuroblastoma

    Research · National Cancer Institute (NCI)

    National Institutes of Health Clinical Center, Bethesda

    Registry updated 2026-10-16

  • NCT06057948

    A Study of a Vaccine in Combination With Beta-glucan in People With Neuroblastoma

    Trial Treatment · Phase 2 · Memorial Sloan Kettering Cancer Center

    Memorial Sloan Kettering at Basking Ridge (Consent Only), Basking Ridge · Memorial Sloan Kettering Suffolk - Commack (Consent Only), Commack · Memorial Sloan Kettering Westchester (Consent only), Harrison · Memorial Sloan Kettering Monmouth (Consent Only), Middletown · Memorial Sloan Kettering Bergen (Consent Only), Montvale · Memorial Sloan Kettering Cancer Center (All Protocol Activities), New York · Memorial Sloan Kettering Nassau (Consent Only), Uniondale

    Registry updated 2026-10-14

  • NCT07087002

    GPC2-CAR T Cell Therapy for Relapsed or Refractory Medulloblastoma in Children and Young Adults

    Trial Treatment · Phase 1 · Stanford University

    Lucile Packard Children's Hospital - Stanford, Palo Alto

    Registry updated 2026-10-09

  • NCT02013336

    Phase 1 Dose-escalating Study of MM-398 (Irinotecan Sucrosofate Liposome Injection) Plus Intravenous Cyclophosphamide in Recurrent or Refractory Pediatric Solid Tumors

    Trial Treatment · Phase 1 · South Plains Oncology Consortium

    Cincinnati Children's Hospital Medical Center, Cincinnati · UT Southwestern, Dallas · Texas Tech University Health Sciences Center, Lubbock · Midwest Children's Hospital, Milwaukee · University of Oklahoma Health Sciences Center, Oklahoma City

    Registry updated 2026-10-08

  • NCT06479811

    Registry updated 2026-10-06

  • NCT06541262

    Silmitasertib (CX-4945) in Combination With Chemotherapy for Relapsed Refractory Solid Tumors

    Trial Treatment · Phase 1/2 · Milton S. Hershey Medical Center

    University of Alabama/Children's of Alabama, Birmingham · Children's Medical Center, Dallas · Children's Hospital of Michigan/Wayne State University, Detroit · University of Florida, Gainesville · Hackensack University Medical Center, Hackensack · Connecticut Children's Hospital, Hartford · Penn State Milton S. Hershey Medical Center and Children's Hospital, Hershey · Kapiolani Medical Center for Women and Children, Honolulu · Children's Mercy Hospitals and Clinics, Kansas City · Norton Children's Research Institute/Affiliated with University of Louisville School of Medicine, Louisville · Nicklaus Children's Hospital, Miami · Monroe Carrell Jr. Children's Hospital at Vanderbilt, Nashville · UCSF Benioff Children's Hospital Oakland, Oakland · Arnold Palmer Hospital for Children, Orlando · Phoenix Children s Hospital, Phoenix · Hasbro Children's Hospital, Providence · Virginia Commonwealth University, Richmond · UC Davis Comprehensive Cancer Center, Sacramento · Primary Children's Hospital, Salt Lake City · Rady Children's Hospital, San Diego · Cardinal Glennon Children's Medical Center, St Louis · All Children's Hospital Johns Hopkins Medicine, St. Petersburg · St. Joseph's Children's Hospital, Tampa

    Registry updated 2026-10-06

  • NCT06721689

    PEEL-224, Vincristine and Temozolomide in Pediatric Solid Tumors

    Trial Treatment · Phase 1/2 · Theodore Laetsch

    Dana-Farber Cancer Institute, Boston · Boston Children's Hospital, Boston · Texas Children's Hospital, Houston · Cedars-Sinai Medical Center, Los Angeles · Children's Hospital of Philadelphia, Philadelphia · University of Utah Hospital, Salt Lake City · University of California San Francisco, San Francisco

    Registry updated 2026-10-06

  • NCT00588068

    Molecular Characterization of Neuroblastic Tumor: Correlation With Clinical Outcome

    Research · Memorial Sloan Kettering Cancer Center

    Memorial Sloan-Kettering Cancer Center, New York

    Registry updated 2026-10-05

  • NCT07527169

    A Phase 2 Study Of Zanzalintinib For Patients With Recurrent Or Metastatic Olfactory Neuroblastoma

    Trial Treatment · Phase 2 · M.D. Anderson Cancer Center

    UT MD Anderson, Houston

    Registry updated 2026-10-05

  • NCT06000787

    MCT for the Harvard/UCSF ROBIN Center

    Trial Treatment · Brigham and Women's Hospital

    Brigham and Women's Hospital, Boston · University of California San Francisco, San Francisco

    Registry updated 2026-10-01

  • NCT04936529

    A Study of a Vaccine in Combination With β-glucan and GM-CSF in People With Neuroblastoma

    Trial Treatment · Phase 2 · Memorial Sloan Kettering Cancer Center

    Memorial Sloan-Kettering Cancer Center, New York

    Registry updated 2026-09-30

  • NCT06674811

    Biomarkers of Resiliency In Childhood Cancer Surgery

    Research · Mayo Clinic

    Mayo Clinic, Rochester

    Registry updated 2026-09-14

All Neuroblastoma trials and the map

This page is not medical advice. Talk to your doctor before contacting a trial.

Neuroblastoma trials in United States – Frontlight Research