Spinal muscular atrophy: open trials in China

11 open trials have a site in China. Registry data; only the trial team decides who can take part.

NCT07221669
A Study to Learn About Salanersen's (BIIB115) Effects on Movement and Its Safety When Given Before Symptoms Appear in Babies With Genetically Diagnosed Spinal Muscular Atrophy (SMA)
Trial Treatment · Phase 3 · Biogen
Guangzhou Woman and Children's Medical Center_Guangzhou, Guangzhou · Childrens Hospital of Fudan University_Shanghai, Shanghai · The Third Affiliated Hospital of Zhengzhou University - North Campus, Zhengzhou
Registry updated 2026-10-23
NCT07822711
Effects of Different Stiffness Settings During Robotic Isokinetic Training in Children With SMA
Trial Treatment · Peking University Third Hospital
Peking University Third Hospital, Beijing
Registry updated 2026-10-23
NCT07554924
A Phase I/II Clinical Study to Evaluate SKG0201 Injection in Subjects With Spinal Muscular Atrophy Type I
Trial Treatment · Phase 1/2 · Lanyue Biotech (Hangzhou) Co., Ltd.
Peking University First Hospital, Beijing · Children's Hospital, Zhejiang University School of Medicine, Hangzhou · Children's Hospital Of Fudan University, Shanghai
Registry updated 2026-10-14
NCT07444476
A Study to Learn About Salanersen's (BIIB115) Effects on Movement and Its Safety in Participants Aged 15 to 60 Years With Spinal Muscular Atrophy (SMA) Who Are Either New to SMA Treatment or Were Previously Treated With Risdiplam
Trial Treatment · Phase 3 · Biogen
Peking Union Medical College Hospital, Beijing
Registry updated 2026-10-02
NCT06772402
GCB-001 in Treatment of Patients With Type II (SMA) Spinal Muscular Atrophy
Trial Treatment · Genecombio Ltd.
Children's Hospital ZheJiang Univisity School Of Medicine, Hangzhou
Registry updated 2026-09-11
NCT05824169
Evaluation of Safety and Efficacy of Gene Therapy Drug in the Treatment of Spinal Muscular Atrophy (SMA) Type 1 Patients
Trial Treatment · Phase 1/2 · GeneCradle Inc
Bayi Children's Hospital, Seventh Medical Center, PLA general hospital, Beijing · Peking University， First Hospital, Department of Pediatrics, Beijing · Shengjing Hospital Of China Medical University, Shenyang · Children's Hospital of Soochow University, Suzhou
Registry updated 2025-07-03
NCT06421831
Evaluation of Safety and Efficacy of Gene Therapy Drug in the Treatment of Spinal Muscular Atrophy (SMA) Type 3 Patients
Trial Treatment · Phase 1/2 · GeneCradle Inc
Beijing Tiantan Hospital,Capital Medical University, Beijing
Registry updated 2025-07-03
NCT06971094
Safety and Efficacy Evaluation of GC101 Gene Therapy Via Intrathecal (IT) Injectionin the Treatment of Patients With Type 2 Spinal Muscular Atrophy (SMA) - Phase III
Trial Treatment · Phase 3 · GeneCradle Inc
Children's Medical Center of Peking University First Hospital, Beijing · Beijing Children's Hospital, Capital Medical University, Beijing · The Seventh Medical Center of Chinese PLA General Hospital, Beijing · National Children's Medical Center，Shanghai Jiaotong University, Shanghai · Shenzhen Children's Hospital, Shenzhen · Children's Hospital of Soochow University, Suzhou · Wuhan Children's Hospital, Tongji Medical College, Huazhong University of Science & Technology, Wuhan
Registry updated 2025-06-05
NCT06888661
Clinical Trial to Assess the Safety and Efficacy of EXG001-307 in Patients With Spinal Muscular Atrophy
Trial Treatment · Early phase 1 · Guangzhou Jiayin Biotech Ltd
The Children's Hospital of Fudan University, Shanghai · Shanghai Children's Medical Center Affiliated to Shanghai Jiao Tong University School of Medicine, Shanghai
Registry updated 2025-03-21
NCT06588803
A Long-term Follow-up Study Evaluating Intravenous Injection of EXG001-307 in Patients With Type 1 SMA
Research · Guangzhou Jiayin Biotech Ltd
The Children's Hospital of Fudan University, Shanghai
Registry updated 2025-03-05
NCT04010604
A Registered Cohort Study on SMA
Research · Wan-Jin Chen
Department of Neurology, First Affiliated Hospital Fujian Medical University, Fuzhou
Registry updated 2019-09-23

All Spinal muscular atrophy trials and the map

This page is not medical advice. Talk to your doctor before contacting a trial.

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