Spinal muscular atrophy: open trials in Italy

9 open trials have a site in Italy. Registry data; only the trial team decides who can take part.

2024-520130-29-00
A Study to Evaluate How Apitegromab Works in Subjects Who Are Less Than 2 Years Old and Have Spinal Muscular Atrophy
Trial Treatment · Phase 2 · Scholar Rock Inc.
Centro Clinico Nemo, Milan · IRCCS Foundation Istituto Neurologico Carlo Besta, Milan · Fondazione Policlinico Universitario Agostino Gemelli IRCCS, Rome
Registry updated 2026-10-29
NCT07221669
A Study to Learn About Salanersen's (BIIB115) Effects on Movement and Its Safety When Given Before Symptoms Appear in Babies With Genetically Diagnosed Spinal Muscular Atrophy (SMA)
Trial Treatment · Phase 3 · Biogen
IRCCS Foundation Istituto Neurologico Carlo Besta, Milan · Centro Clinico Nemo, Milan
Registry updated 2026-10-23
NCT07883655
Advanced Multi-omics and -System Approaches to Identify Novel Biomarkers for SMA
Research · Istituto Giannina Gaslini
IRCCS Istituto Giannina Gaslini, Genova · Fondazione Ca' Granda Ospedale Maggiore Policlinico, Milan · Istituto di Bioscienze e Biorisorse IBBR, Naples
Registry updated 2026-10-20
NCT07444450
A Study to Learn About the Safety and Effects of Salanersen (BIIB115) When Given to Babies With Spinal Muscular Atrophy (SMA) Who Were Previously Treated With Onasemnogene Abeparvovec
Trial Treatment · Phase 3 · Biogen
Centro Clinico Nemo, Milan · IRCCS Foundation Istituto Neurologico Carlo Besta, Milan · Fondazione Policlinico Universitario Agostino Gemelli IRCCS, Rome
Registry updated 2026-10-15
NCT07047144
A Study to Evaluate How Apitegromab Works in Subjects Who Are Less Than 2 Years Old and Have Spinal Muscular Atrophy
Trial Treatment · Phase 2 · Scholar Rock, Inc.
Centro Clinico NeMO Milano - Fondazione Serena Onlus, Milan · Fondazione I.R.C.C.S. Istituto Neurologico Carlo Besta, Milan · Fondazione Policlinico Universitario Agostino Gemelli IRCCS, Rome
Registry updated 2026-10-02
NCT06555419
A Study to Find Out How Nusinersen is Processed in the Body When Given Through the ThecaFlex DRx™ System in Adult and Pediatric Participants With Spinal Muscular Atrophy (PIERRE-PK)
Trial Treatment · Phase 1 · Biogen
Centro Clinico Nemo, Milan · Fondazione Policlinico Universitario Agostino Gemelli IRCCS, Rome
Registry updated 2026-09-03
NCT06666816
Observational Study to Observe Variations of Gait Parameters in Patients With Neuromuscular Diseases
Research · IRCCS Eugenio Medea
Scientific Institute IRCCS E. Medea - Sede di Bosisio Parini, Bosisio Parini · Scientific Institute IRCCS E. Medea - Polo di Conegliano, Conegliano
Registry updated 2026-01-20
NCT05768048
Long Term Trajectories of SMA Patients Receiving or Not Disease-modifying Treatments
Research · Fondazione Policlinico Universitario Agostino Gemelli IRCCS
Istituto Gaslini, Genova · Nemo Sud, Messina · Centro Clinico Nemo, Milan · Ospedale Bambino gesu, Rome · Policlinico Gemelli, Rome
Registry updated 2023-03-14
NCT05755451
Natural History of SMA
Research · Fondazione Policlinico Universitario Agostino Gemelli IRCCS
Istituto Gaslini, Genova · Nemo Sud, Messina · Centro Clinico Nemo, Milan · Ospedale Bambino gesu, Rome · Policlinico Gemelli, Rome
Registry updated 2023-03-06

All Spinal muscular atrophy trials and the map

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