Helen DeVos Children's Hospital

The trials here

What the 30 trials at this site are about, from their registry records.

Conditions

• Childhood cancers11 trials
• Cystic fibrosis6 trials
• Neuroblastoma6 trials
• Spinal muscular atrophy4 trials
• Acute lymphoblastic leukaemia3 trials
• Aplastic anaemia2 trials
• Duchenne muscular dystrophy2 trials
• Sarcoma2 trials
• Acute myeloid leukaemia1 trial
• Chronic lymphocytic leukaemia1 trial
• Chronic myeloid leukaemia1 trial
• Congenital heart disease1 trial
• and 12 more

Phase

• Phase 25 trials
• Phase 33 trials
• Phase 12 trials
• Phase 1/22 trials
• Phase 42 trials
• Phase 2/31 trial

Status

• Recruiting11 trials
• Completed9 trials
• Active, not recruiting7 trials
• Enrolling by invitation1 trial
• Not yet recruiting1 trial
• Terminated1 trial

Lead sponsor

• Giselle Sholler6 trials
• Scholar Rock, Inc.3 trials
• Chris Goss2 trials
• Nicole Hamblett2 trials
• Alcyone Therapeutics, Inc1 trial
• and 16 more

Running trials

• Recruiting

  Metastatic Ewing's Trial Testing Schedule Enhancement to Improve Outcomes

  NCT07194044· Phase 1· H. Lee Moffitt Cancer Center and Research Institute· Source

  Contact: David Hoogstra, MD (principal investigator)

• Recruiting

  Registry Study to Observe Long-term Safety of Vamorolone (AGAMREE®) in Patients With Duchenne Muscular Dystrophy-SUMMIT

  NCT06564974· Catalyst Pharmaceuticals, Inc.· Source

  Contact: Mark Wingertzahn, PhD

• Recruiting

  Transforming Care for Individuals With Childhood-onset Systemic Lupus Erythematosus

  NCT06232304· Michigan State University· Source

  Contact: Jocelyn S Zuckerman

• Recruiting

  Study of an Intrathecal Port and Catheter System for Subjects With Spinal Muscular Atrophy

  NCT05866419· Alcyone Therapeutics, Inc· Source

  Contact: Natasha Schafer

• Recruiting

  Targeted Immunotherapy After Myeloablative TBI-Based Conditioning & AlloHCT in CAYA With High Risk T-Cell ALL & Lymphoma

  NCT04972942· Phase 1· New York Medical College· Source

  Contact: Troy Quigg, DO

• Recruiting

  Standardizing Treatments for Pulmonary Exacerbations - Aminoglycoside Study

  NCT05548283· Phase 4· Chris Goss· Source

  Contact: Andrew James

• Active, not recruiting

  Long-Term Safety & Efficacy of Apitegromab in Patients With SMA Who Completed Previous Trials of Apitegromab

  NCT05626855· Phase 3· Scholar Rock, Inc.· Source

• Active, not recruiting

  AFFINITY DUCHENNE: RGX-202 Gene Therapy in Participants With Duchenne Muscular Dystrophy (DMD)

  NCT05693142· Phase 2/3· REGENXBIO Inc.· Source

• Recruiting

  Adult Congenital Heart Disease International EValuation of the Effectiveness of SGLT2i Registry

  NCT06932081· Leiden University Medical Center· Source

  Contact: Gruschen R. Veldtman, MBChB FRCP (principal investigator)

• Active, not recruiting

  Prospective Study of Pregnancy in Women With Cystic Fibrosis

  NCT04828382· Amalia Magaret· Source

• Recruiting

  Study to Evaluate Biological & Clinical Effects of Significantly Corrected CFTR Function in Infants & Young Children

  NCT04509050· Sonya Heltshe· Source

  Contact: Andrew James

• Active, not recruiting

  Eflornithine (DFMO) and Etoposide for Relapsed/Refractory Neuroblastoma

  NCT04301843· Phase 2· Giselle Sholler· Source

• Active, not recruiting

  CHaractErizing CFTR Modulated Changes in Sweat Chloride and Their Association With Clinical Outcomes

  NCT03350828· Nicole Hamblett· Source

• Recruiting

  Reduced Intensity Conditioning and Familial HLA-Mismatched BMT for Non-Malignant Disorders

  NCT03128996· Phase 1/2· Washington University School of Medicine· Source

  Contact: Troy Quigg, DO

• Active, not recruiting

  Neuroblastoma Maintenance Therapy Trial

  NCT02679144· Phase 2· Giselle Sholler· Source

• Recruiting

  Pediatric Precision Laboratory Advanced Neuroblastoma Therapy

  NCT02559778· Phase 2· Giselle Sholler· Source

  Contact: Mary Beth Readwin

• Active, not recruiting

  HeadStart4: Newly Diagnosed Children (<10 y/o) With Medulloblastoma and Other CNS Embryonal Tumors

  NCT02875314· Phase 4· Parth Patel· Source

• Recruiting

  Observational Study of Pediatric Rheumatic Diseases: The CARRA Registry

  NCT02418442· Duke University· Source

  Contact: Genesis Pablo Mendoza

• Recruiting

  Antiangiogenic Therapy for Children With Recurrent Medulloblastoma, Ependymoma, ATRT and Rare CNS Tumors

  NCT01356290· Phase 2· Medical University of Vienna· Source

  Contact: Rebecca Loret de Mola

• Recruiting

  A Multicenter Access and Distribution Protocol for Unlicensed Cryopreserved Cord Blood Units (CBUs)

  NCT01351545· Center for International Blood and Marrow Transplant Research· Source

  Contact: Troy Quigg, MD

Recruiting at the same time

How many trials recruit for the same indication here at once. A count, not a rating.

• Childhood cancers5 recruiting
• Acute lymphoblastic leukaemia2 recruiting
• Cystic fibrosis2 recruiting
• Acute myeloid leukaemia1 recruiting
• Aplastic anaemia1 recruiting
• Chronic lymphocytic leukaemia1 recruiting
• Chronic myeloid leukaemia1 recruiting
• Congenital heart disease1 recruiting
• Duchenne muscular dystrophy1 recruiting
• Heart failure1 recruiting
• Hodgkin lymphoma1 recruiting
• Lupus (SLE)1 recruiting
• Multiple myeloma1 recruiting
• Neuroblastoma1 recruiting
• Psoriasis1 recruiting
• Psoriatic arthritis1 recruiting
• Rheumatoid arthritis1 recruiting
• Sarcoma1 recruiting
• Sickle cell disease1 recruiting
• Spinal muscular atrophy1 recruiting

Closed trials

• Terminated

  A Trial Comparing Unrelated Donor BMT With IST for Pediatric and Young Adult Patients With Severe Aplastic Anemia (TransIT, BMT CTN 2202)

  NCT05600426· Phase 3· Boston Children's Hospital· Source

• Completed

  Observational Study Comparing Home to Office Spirometry

  NCT05285410· Chris Goss· Source

• Completed

  Vaccine Immune Recovery After Leukemia

  NCT05622682· Children's Hospital of Philadelphia· Source

• Completed

  Efficacy and Safety of Apitegromab in Patients With Later-Onset Spinal Muscular Atrophy Treated With Nusinersen or Risdiplam

  NCT05156320· Phase 3· Scholar Rock, Inc.· Source

• Completed

  A Prospective Study to Evaluate Biological and Clinical Effects of Significantly Corrected CFTR Function

  NCT04038047· Nicole Hamblett· Source

• Completed

  An Active Treatment Study of SRK-015 in Patients With Type 2 or Type 3 Spinal Muscular Atrophy

  NCT03921528· Phase 2· Scholar Rock, Inc.· Source

• Completed

  Molecular-Guided Therapy for Childhood Cancer

  NCT02162732· Giselle Sholler· Source

• Completed

  Study of Difluoromethylornithine (DFMO) in Combination With Bortezomib for Relapsed or Refractory Neuroblastoma

  NCT02139397· Phase 1/2· Giselle Sholler· Source

• Completed

  Pediatric Obesity Weight Evaluation Registry (POWER) Study

  NCT02121132· Children's Hospital Medical Center, Cincinnati· Source

• Completed

  Molecular-Guided Therapy for Relapsed and Refractory Childhood Cancer

  NCT01802567· Giselle Sholler· Source