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Cystic fibrosis: open trials in United States

83 open trials have a site in United States. Registry data; only the trial team decides who can take part.

  • NCT00001532

    Role of Genetic Factors in the Development of Lung Disease

    Research · National Heart, Lung, and Blood Institute (NHLBI)

    Suburban Hospital, Bethesda · National Institutes of Health Clinical Center, Bethesda

    Registry updated 2026-11-09

  • NCT00943514

    Natural History of Bronchiectasis

    Research · National Heart, Lung, and Blood Institute (NHLBI)

    National Institutes of Health Clinical Center, Bethesda

    Registry updated 2026-11-09

  • NCT02417740

    Natural History of Noncirrhotic Portal Hypertension

    Research · National Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)

    National Institutes of Health Clinical Center, Bethesda

    Registry updated 2026-11-09

  • NCT06654752

    Streamlined Treatment of Pulmonary Exacerbations in Pediatrics

    Trial Treatment · University of Washington, the Collaborative Health Studies Coordinating Center

    University of Michigan Health System, Ann Arbor · Children's Healthcare of Atlanta, Emory University, Atlanta · Children's Hospital of Colorado, Aurora · Johns Hopkins Hospital, Johns Hopkins University, Baltimore · The Children's Hospital Alabama & University of Alabama at Birmingham, Birmingham · Boston Children's Hospital, Harvard University, Boston · Vermont Children's Hospital & University of Vermont Medical Center, Burlington · University of North Carolina at Chapel Hill, Chapel Hill · Medical University of South Carolina, Charleston · Ann & Robert H. Lurie Children's Hospital of Chicago & Northwestern University, Chicago · Cincinnati Children's Hospital Medical Center, Cincinnati · University of Texas Southwestern, Children's Health, Dallas · Texas Children's Hospital/ Baylor College of Medicine, Houston · Riley Hospital for Children - Indiana University, Indianapolis · University of Iowa, Iowa City · Children's Mercy Hospital, Kansas City · Children's Hospital of Los Angeles & Anton Yelchin Cystic Fibrosis Clinic, Los Angeles · University of Wisconsin, Madison · Children's Wisconsin & Medical College of Wisconsin, Milwaukee · The Minnesota Cystic Fibrosis Center & University of Minnesota, Minneapolis · Children's Hospitals and Clinics of Minnesota, Minneapolis · Stanford University, Palo Alto · Children's Hospital of Philadelphia & University of Pennsylvania, Philadelphia · Children's Hospital of Pittsburgh of UPMC & University of Pittsburgh Medical Center, Pittsburgh · Oregon Health Science University, Portland · Virginia Commonwealth University, Richmond · University of Rochester Medical Center Strong Memorial, Rochester · Rady Children's Hospital at University of California San Diego, San Diego · Seattle Children's Hospital, Seattle · St. Louis Children's Hospital - Washington University School of Medicine, St Louis · Tucson Cystic Fibrosis Center, Tucson

    Registry updated 2026-11-09

  • NCT07720375

    A Study of 24 to 52 Weeks Treatment to Evaluate The Efficacy And Safety of Galvokimig in Adult Study Participants With Non-Cystic Fibrosis Bronchiectasis

    Trial Treatment · Phase 2 · UCB Biopharma SRL

    Ncfb01 50003, Brandon · Ncfb01 50004, DuBois · Ncfb01 50001, McKinney · Ncfb01 50010, Mesquite · Ncfb01 50012, Newport Beach · Ncfb01 50005, Plantation · Ncfb01 50007, Rock Hill

    Registry updated 2026-11-06

  • NCT05686837

    Prospective Healthcare-Associated Links in Transmission of Nontuberculous Mycobacteria

    Research · University of North Carolina, Chapel Hill

    Dell Children's Ascension, Austin · Johns Hopkins Cystic Fibrosis Center, Baltimore · UVA Health University Medical Center, Charlottesville · The University of Vermont Medical Center, Colchester · UT Southwestern Medical Center, Dallas · National Jewish Health, Denver · UW Medical Center, Seattle

    Registry updated 2026-11-03

  • NCT07048574

    TIDES 2.0: Prevalence and Longitudinal Course of Depression, Anxiety, and Behavior Problems in Children With Cystic Fibrosis Under 12 Years of Age

    Research · State University of New York at Buffalo

    Children's Hospital Colorado, Aurora · Indiana University, Bloomington · Massachusetts General Hospital, Boston · University at Buffalo, Buffalo · University of North Carolina School of Medicine, Chapel Hill · Cincinnati Children's Hospital Medical Center, Cincinnati · Joe DiMaggio, Hollywood · Children's Hospital of Orange County, Orange · Nemours Foundation, Orlando · UT Southwestern, Plano · Brown University Health, Providence · Children's Hospital of Richmond at Virginia Commonwealth University, Richmond · Seattle Children's Hospital, Seattle

    Registry updated 2026-11-03

  • NCT07450547

    Phase 2 Study to Assess the Safety and Efficacy of ANG003

    Trial Treatment · Phase 2 · Anagram Therapeutics, Inc.

    Children's Hospital Medical Center of Akron, Akron · University of Michigan - Michigan Medicine, Ann Arbor · Emory-Children's Healthcare of Atlanta Cystic Fibrosis Center, Atlanta · Massachusetts General Hospital, Boston · Boston Children's Hospita, Boston · Rainbow Babies and Children's Hospital / University Hospitals Cleveland Medical Center, Cleveland · Nationwide Children's Hospital, Columbus, Columbus · University of Texas Southwestern, Children's Health, Dallas · National Jewish Health, Denver · Wayne State University Harper University Hospital, Detroit · University of Florida, Gainesville · The Cystic Fibrosis Institute, Glenview · Hershey Medical Center Pennsylvania State University, Hershey · University of Iowa, Iowa City · University of Kansas Medical Center, Kansas City · University of Kentucky, Lexington · Long Beach Memorial Medical Center, Long Beach · Center for Cystic Fibrosis at Keck Medical Center of USC, Los Angeles · University of Wisconsin, Madison · Froedtert & Medical College of Wisconsin, Milwaukee · University of Minnesota, Minneapolis · Rutgers, Robert Wood Johnson Medical School, New Brunswick · Central Florida Pulmonary Group, Orlando · University of Pittsburgh Medical Center, Pittsburgh · MaineHealth Pediatric Specialty Care, Portland · Adult Cystic Fibrosis Center at the University of Utah, Salt Lake City · Toledo Children's Hospital, Toledo · New York Medical College at Westchester Medical Center, Valhalla

    Registry updated 2026-10-30

  • NCT07903311

    Iron Repletion in Cystic Fibrosis

    Trial Treatment · Phase 4 · University of Michigan

    University of Michigan, Ann Arbor · Medical University of South Carolina, Charleston · National Jewish Health, Denver · Indiana University, Indianapolis · The University of Kansas Medical Center, Kansas City · University of Minnesota, Minneapolis · Columbia University Irving Medical Center, New York · University of Nebraska Medical Center, Omaha

    Registry updated 2026-10-29

  • NCT06559150

    A Phase II Study of Ensifentrine in Non-Cystic Fibrosis Bronchiectasis

    Trial Treatment · Phase 2 · Verona Pharma, Inc., a subsidiary of Merck & Co., Inc. (Rahway, New Jersey USA

    University of Michigan Hospital, Ann Arbor · Emory University at Saint Joseph Pulmonary Clinic, Atlanta · Augusta University, Augusta · Kirklin Clinic of UAB Hospital, Birmingham · Massachusetts General Hospital- 55 Fruit St, Boston · University of North Carolina, Chapel Hill · Medical University of South Carolina (MUSC) - PPDS, Charleston · Ohio State University, Columbus · National Jewish Health-Main Campus, Denver · Clinical Trials Center of Middle Tennessee, Franklin · ASHA Clinical Research, Hammond · The Respire Institute, Houston · University of Iowa, Iowa City · University of Kansas Medical Center-Kansas City, Kansas City · So Cal Institute for Respiratory Diseases, Inc., Los Angeles · University of Miami, Miami · NYU Langone Health Pulmonary and Critical Care Associates, P.C. - BRANY - PPDS, New York · Temple University Hospital, Philadelphia · Oregon Health and Science University, Portland · Mayo Clinic, Rochester · University of California, Davis Medical Center, Sacramento · Velocity Clinical Research - Spartanburg - PPDS, Spartanburg · Washington University School of Medicine, St Louis · UT Texas Health Science at Tyler, Tyler · Velocity Clinical Research - Union - PPDS, Union · MedStar Georgetown University Hospital, Washington D.C. · TPMG Clinical Research, Williamsburg · Accellacare of Wilmington, Wilmington · Southeastern Research Center, Winston-Salem

    Registry updated 2026-10-27

  • NCT07414810

    Novel Point-of-care Sweat Chloride Testing Device for Monitoring CFTR Function

    Trial Treatment · Emory University

    Arthur M Blank Hospital - Children's Healthcare of Atlanta, Atlanta · Adult Cystic Fibrosis Clinic, Atlanta

    Registry updated 2026-10-27

  • NCT07283770

    Evaluation of VX-581 in Healthy Participants and in Participants With Cystic Fibrosis

    Trial Treatment · Phase 1 · Vertex Pharmaceuticals Incorporated

    Altasciences - Kansas City, Overland Park

    Registry updated 2026-10-19

  • NCT07275905

    Bacteriophages for Adults With Cystic Fibrosis and Chronic Achromobacter Lung Infection

    Trial Treatment · Phase 1 · Ghady Haidar

    University of Pittsburgh, Pittsburgh

    Registry updated 2026-10-08

  • NCT04793867

    Regional Phenotyping of CF and Non-CF Bronchiectasis

    Research · Children's Hospital Medical Center, Cincinnati

    Penny New, Cincinnati

    Registry updated 2026-10-07

  • NCT06296394

    Health Outcomes of Parents With Cystic Fibrosis-Aim 2

    Research · University of Pittsburgh

    University of Michigan, Ann Arbor · Johns Hopkins University, Baltimore · University of Alabama Birmingham, Birmingham · Massachusetts General Hospital, Boston · Boston Children's Hospital/Brigham and Women's Hospital, Boston · University of North Carolina, Chapel Hill · Medical University of South Carolina, Charleston · University of Texas, Southwestern, Dallas · National Jewish Health, Denver · Northwestern University, Evanston · Indiana University, Indianapolis · University of Kansas Medical Center, Kansas City · University of Minnesota, Minneapolis · University of Pennsylvania, Philadelphia · University of Pittsburgh, Pittsburgh · Oregon Health and Science University, Portland · University of Washington, Seattle · Washington University School of Medicine, St Louis

    Registry updated 2026-10-07

  • NCT06512064

    Acoustic Waveform Respiratory Evaluation

    Trial Treatment · Indiana University

    Indiana University, Indianapolis · University of Pittsburgh, Pittsburgh

    Registry updated 2026-10-05

  • NCT05359991

    Exercise in Child Health

    Trial Treatment · University of California, Irvine

    University of California, Irvine, Irvine

    Registry updated 2026-10-02

  • NCT07559175

    A Study to Evaluate Safety and Explore Efficacy of New Lipase NHS7108 in Adult Participants With Exocrine Pancreatic Insufficiency.

    Trial Treatment · Phase 2 · Aimmune Nestlé Health Science US R&D, LLC

    Johns Hopkins Medicine - Pulmonary and Critical Care, Baltimore · Billings Clinic Hospital - Public, Billings · University Hospitals Cleveland Medical Center Rainbow Babies & Children's Hospital, Cleveland · The Ohio State University College of Medicine (OSUCOM), Columbus · Omnicure Clinical Research, Doral · Penn State Health, Hershey · Johnson County Clin-Trials (JCCT), Lenexa · University of Arkansas for Medical Sciences Hospital - University, Little Rock · Cedars Sinai Medical Center - Inflammatory Bowel Disease Ctr, Los Angeles · Keck Hospital of USC, Los Angeles · Vanderbilt University Medical Center - Pulmonary Hospital - University, Nashville · University of Oklahoma Health Sciences Center - Pediatrics Hospital - University, Oklahoma City · Advent Health Medical Group, Orlando · HonorHealth Research Institute, Scottsdale

    Registry updated 2026-10-01

  • NCT05463289

    ACCESS 2: AI for pediatriC diabetiC Eye examS Study 2

    Trial Treatment · Johns Hopkins University

    Johns Hopkins Pediatric Diabetes Center, Baltimore

    Registry updated 2026-09-23

  • NCT07163078

    Nutrition Supplement for Cystic Fibrosis

    Trial Treatment · Ohio State University

    Nationwide Children's Hospital/ Ohio State University, Columbus

    Registry updated 2026-09-21

  • NCT04930289

    Global Utilization And Registry Database for Improved preservAtion of doNor LUNGs

    Research · Paragonix Technologies

    Johns Hopkins University, Baltimore · Massachusetts General Hospital, Boston · University of Virginia, Charlottesville · Baylor Scott & White Research Institute, Dallas · The University of Texas Southwestern Medical Center, Dallas · Duke Lung Transplant Clinic, Durham · Houston Methodist Hospital, Houston · Mayo Clinic- Jacksonville, Jacksonville · Temple University Hospital, Philadelphia · St. Joseph's Hospital and Medical Center, Phoenix · University of Pittsburgh Medical Center, Pittsburgh · University of California San Francisco, San Francisco · Stanford Medicine, Stanford · Montefiore Hospital, The Bronx

    Registry updated 2026-09-18

  • NCT01852448

    Genetics of Insulin and Incretins in Cystic Fibrosis

    Research · Children's Hospital of Philadelphia

    The Children's Hopsital of Philadelphia, Philadelphia · The University of Pennsylvania, Philadelphia

    Registry updated 2026-09-16

  • NCT04469439

    Impact of Sinus Surgery on Individuals With Cystic Fibrosis

    Research · University of California, Los Angeles

    University of Colorado, Aurora · University of North Carolina, Chapel Hill · Medical University of South Carolina, Charleston · National Jewish Health, Denver · University of California, Los Angeles, Los Angeles · Vanderbilt University Medical Center, Nashville · Oregon Health Science University, Portland · University of Utah, Salt Lake City · Stanford University, Stanford

    Registry updated 2026-09-10

  • NCT06191640

    Sinus Disease in Young Children With Cystic Fibrosis

    Research · University of California, Los Angeles

    Children's Hospital Colorado, Aurora · University of Virginia, Charlottesville · Cincinnati Children's Hospital Medical Center, Cincinnati · University of Vermont, Colchester · University of Iowa, Iowa City · University of Kansas Medical Center, Kansas City

    Registry updated 2026-09-10

  • NCT06995651

    Dorzagliatin in Pancreatic Insufficient Cystic Fibrosis

    Trial Treatment · Phase 1 · Michael R. Rickels, MD, MS

    Hospital of University of Pennsylvania, Philadelphia · University of Pennsylvania Center for Human Phenomic Science (CHPS), Philadelphia

    Registry updated 2026-08-31

All Cystic fibrosis trials and the map

This page is not medical advice. Talk to your doctor before contacting a trial.

Under construction, not live – Cystic fibrosis trials in United States – Frontlight Research