Duchenne muscular dystrophy trials in Australia

4 trials · From ClinicalTrials.gov, checked 12 November 2026. Ask the study team whether a trial fits you.

• Phase 3Taking people
  A Phase 3 Study to Evaluate the Safety and Efficacy of AOC 1044 (Also Referred to as Delpacibart Zotadirsen) in Participants With DMD With Gene Mutations Amenable to Exon 44 Skipping

  Where

  Westmead

  Age

  7 years to 16 years

  People

  70 worldwide

  Run by

  Avidity Biosciences, Inc.

  See details and how to joinNCT07587242
• Phase 2Enrolling by invitation
  An Open-label Long-term Follow-up Study of SAT-3247 for Participants With Duchenne Muscular Dystrophy Including Those Who Participated in SAT-3247-CL-101

  Where

  Melbourne

  Age

  16 years to 40 years

  People

  30 worldwide

  Run by

  Satellos Bioscience, Inc.

  See details and how to joinNCT06867107
• Phase 3Taking people
  A Study of SGT-003 Gene Therapy in Ambulant Males With Duchenne Muscular Dystrophy (IMPACT DUCHENNE)

  Where

  Sydney

  Age

  7 years to 11 years

  People

  80 worldwide

  Run by

  Solid Biosciences Inc.

  See details and how to joinNCT07160634 · EU 2025-522949-22-00
• Phase 2Enrolling by invitation
  Open-Label Extension of EDG-5506 in Participants With Becker Muscular Dystrophy

  Where

  Melbourne

  People

  260 worldwide

  Run by

  Edgewise Therapeutics, Inc.

  See details and how to joinNCT06066580