Duchenne muscular dystrophy trials in Germany
10 trials · From ClinicalTrials.gov and EU CTIS (euclinicaltrials.eu), checked 12 November 2026. Ask the study team whether a trial fits you.
- Phase 3Taking peopleA Phase 3 Study to Evaluate the Safety and Efficacy of AOC 1044 (Also Referred to as Delpacibart Zotadirsen) in Participants With DMD With Gene Mutations Amenable to Exon 44 Skipping
- Where
- Essen, Heidelberg, München
- Age
- 7 years to 16 years
- People
- 70 worldwide
- Run by
- Avidity Biosciences, Inc.
See details and how to joinNCT07587242 - Phase 3Taking peopleStudy in which all the patients take the same investigational drug with the aim of evaluate the long-term safety, tolerability, and efficacy of GIVINOSTAT in all the patients affected with Duchenne Muscolar Dystrophy who have been already treated in one of the GIVINOSTAT studies in the past
- Where
- Berlin, Essen, Freiburg im Breisgau, Hamburg, Munich
- Age
- Up to 64 years
- People
- 207 worldwide
- Run by
- Italfarmaco S.p.A.
See details and how to join2023-504520-26-00 · EU 2023-504520-26-00 - No phaseTaking peopleRegistry for Duchenne and Becker Muscular Dystrophy
- Where
- Berlin, Bochum, Bonn, Bremen, Dresden, Erlangen, Essen, Freiburg im Breisgau, Giessen, Göttingen, Greifswald, Hamburg, Hanover, Heidelberg, Homburg, Jena, Kassel, Leipzig, München, Münster, Stuttgart, Tübingen, Ulm
- People
- 1,500 worldwide
- Run by
- Dr. Andreas Ziegler
See details and how to joinNCT07402122 - Phase 3Taking peopleA Study of SGT-003 Gene Therapy in Ambulant Males With Duchenne Muscular Dystrophy (IMPACT DUCHENNE)
- Where
- Essen, Freiburg im Breisgau, Munich
- Age
- 7 years to 11 years
- People
- 80 worldwide
- Run by
- Solid Biosciences Inc.
See details and how to joinNCT07160634 · EU 2025-522949-22-00 - Phase 2Enrolling by invitationOpen-Label Extension of EDG-5506 in Participants With Becker Muscular Dystrophy
- Where
- Munich
- People
- 260 worldwide
- Run by
- Edgewise Therapeutics, Inc.
See details and how to joinNCT06066580 - Phase 1/2Taking peopleA Study in Participants With Duchenne Muscular Dystrophy Amenable to Exon 44 Skipping to Evaluate the Safety and Efficacy of ENTR-601-44
- Where
- Essen, Goettingen
- Age
- 4 years to 20 years
- People
- 24 worldwide
- Run by
- Entrada Therapeutics, Inc.
See details and how to joinNCT07037862 · EU 2024-517584-23-00 - Phase 3Taking peopleEfficacy, Safety and Tolerability of Givinostat in Non-ambulant Patients With Duchenne Muscular Dystrophy
- Where
- Berlin, Essen, Freiburg im Breisgau, Hamburg
- Age
- 9 years to 17 years
- People
- 138 worldwide
- Run by
- Italfarmaco
See details and how to joinNCT05933057 · EU 2023-503521-19-00 - Phase 3Taking peopleA Phase 3, Randomized, Double-Blind, Placebo-Controlled, Global Study with an Open-Label Extension to Evaluate the Efficacy and Safety of Intravenous AOC 1044 (delpacibart zotadirsen) for the Treatment of DMD with Gene Mutations Amenable to Exon 44 Skipping
- Where
- Essen, Heidelberg, Munich
- Age
- Up to 17 years
- People
- 42 worldwide
- Run by
- Avidity Biosciences Inc.
See details and how to join2025-523087-20-00 · EU 2025-523087-20-00 - Phase 3Enrolling by invitationA Long-term Follow-up Study of Participants Who Received Delandistrogene Moxeparvovec (SRP-9001) in a Previous Clinical Study
- Where
- Essen
- Age
- Up to 64 years
- People
- 400 worldwide
- Run by
- Sarepta Therapeutics, Inc.
See details and how to joinNCT05967351 · EU 2023-505043-39-00 - Phase 2/3Taking peopleGivinostat in Duchenne's Muscular Dystrophy Long-term Safety and Tolerability Study
- Where
- Essen, Hamburg, München
- Age
- 7 years and over
- People
- 206 worldwide
- Run by
- Italfarmaco
See details and how to joinNCT03373968