Fabry disease trials in Japan

3 trials · From ClinicalTrials.gov, checked 11 November 2026. Ask the study team whether a trial fits you.

• Phase 3Taking people
  A Study of Migalastat in Pediatric Subjects (2 to <12 Yrs) With Fabry Disease and Amenable GLA Variants

  Where

  Sagamihara

  Age

  2 years to 11 years

  People

  8 worldwide

  Run by

  Amicus Therapeutics

  See details and how to joinNCT06904261
• No phaseTaking people
  Fabry Disease Registry & Pregnancy Sub-registry

  Where

  Chiba, Kobe, Nankoku, Niigata, Osaka, Tokyo

  People

  9,000 worldwide

  Run by

  Genzyme, a Sanofi Company

  See details and how to joinNCT00196742
• Phase 2/3Taking people
  Study to Evaluate the Safety, PK, PD, and Efficacy of PRX-102 in Japanese Patients With Fabry Disease

  Where

  Asahikawa, Bunkyo-ku, Chikushino-shi, Minato-ku, Niigata, Nishihara, Okayama, Sendai, Shinjuku-ku, Suita

  Age

  13 years to 70 years

  People

  16

  Run by

  Chiesi Farmaceutici S.p.A.

  See details and how to joinNCT05710692