Gaucher disease trials in Pakistan

2 trials · From ClinicalTrials.gov, checked 13 November 2026. Ask the study team whether a trial fits you.

• Phase 2Not yet taking people in Pakistan
  Study to Evaluate the Efficacy and Safety of Nizubaglustat (AZ-3102) in Patients With Gaucher Disease Type 3 (GD3)

  Where

  Lahore, Peshawar

  Age

  4 years to 30 years

  People

  20 worldwide

  Run by

  Azafaros B.V.

  See details and how to joinNCT07715084
• No phaseTaking people
  International Collaborative Gaucher Group (ICGG) Gaucher Disease Registry & Pregnancy Sub-registry

  Where

  Karachi, Lahore

  People

  12,000 worldwide

  Run by

  Genzyme, a Sanofi Company

  See details and how to joinNCT00358943