Gaucher disease trials in Portugal

2 trials · From ClinicalTrials.gov, checked 13 November 2026. Ask the study team whether a trial fits you.

• No phaseTaking people
  International Collaborative Gaucher Group (ICGG) Gaucher Disease Registry & Pregnancy Sub-registry

  Where

  Coimbra, Lisbon, Ponta Delgada

  People

  12,000 worldwide

  Run by

  Genzyme, a Sanofi Company

  See details and how to joinNCT00358943
• Phase 3Taking people
  A Gaucher Disease Gene Therapy Trial With FLT201

  Where

  Lisbon

  Age

  18 years and over

  People

  45 worldwide

  Run by

  Spur Therapeutics

  See details and how to joinNCT07223944 · EU 2025-520765-50-00