Haemophilia trials in Australia

In Australia 10 Also abroad 128

10 trials · From ClinicalTrials.gov, checked 11 November 2026. Ask the study team whether a trial fits you.

Phase 4Taking people
Efanesoctocog Alfa Prophylaxis in Patients With Hemophilia A With Synovial Hypertrophy
Where
Murdoch
Age
12 years and over
People
35 worldwide
Run by
Sanofi
See details and how to joinNCT06941870
Phase 3Taking people
A Clinical Study to Evaluate the Effects of NXT007 Compared to Emicizumab Prophylaxis in People With Hemophilia A
Where
Camperdown, Melbourne, Parkville
Age
12 years and over
People
360 worldwide
Run by
Hoffmann-La Roche
See details and how to joinNCT07416604 · EU 2025-522435-33-00
Phase 3Taking people
A Research Study Investigating Denecimig (Mim8) in Adults With Acquired Haemophilia A
Where
Camperdown, Herston, Melbourne
Age
18 years and over
People
84 worldwide
Run by
Novo Nordisk A/S
See details and how to joinNCT07830732 · EU 2026-525529-19-00
Phase 3Taking people
Open-Label Extension Study of Marstacimab in Hemophilia Participants With or Without Inhibitors
Where
Melbourne
Age
1 year to 74 years
People
245 worldwide
Run by
Pfizer
See details and how to joinNCT05145127 · EU 2022-500470-33-00
Phase 1/2Taking people
A Study to Investigate the Safety and Effectiveness of a Coagulation Factor IX Gene Insertion Therapy (REGV131-LNP1265) in Pediatric, Adolescent and Adult Participants With Hemophilia B
Where
Adelaide, Camperdown, Herston, Melbourne
Age
2 years and over
People
130 worldwide
Run by
Regeneron Pharmaceuticals
See details and how to joinNCT06379789 · EU 2023-507260-40-00
Phase 3Taking people
Phase 3, Open-label, Single-dose Study of CSL222 in Adolescent Male Subjects (≥ 12 to < 18 Years of Age) With Severe or Moderately Severe Hemophilia B
Where
Brisbane, Westmead
Age
138 months to 206 months
People
20 worldwide
Run by
CSL Behring
See details and how to joinNCT07080905 · EU 2023-505805-18-00
Phase 3Taking people
A Clinical Trial of Study Medicine (Marstacimab) in Pediatric Patients With Hemophilia A or Hemophilia B
Where
Parkville
Age
1 year to 17 years
People
100 worldwide
Run by
Pfizer
See details and how to joinNCT05611801 · EU 2022-500495-65-00
Phase 3Taking people
Safety and Effectiveness of Giroctocogene Fitelparvovec or Fidanacogene Elaparvovec in Patients With Hemophilia A or B Respectively
Where
Camperdown, Melbourne
Age
18 years and over
People
173 worldwide
Run by
Pfizer
See details and how to joinNCT05568719
Phase 3Taking people
Efficacy and Safety of CSL222 (Etranacogene Dezaparvovec) Gene Therapy in Adults With Hemophilia B With Pretreatment Adeno-associated Virus Serotype 5 (AAV5) Neutralizing Antibodies (Nabs)
Where
Adelaide, Camperdown, Herston, Melbourne
Age
18 years and over
People
35 worldwide
Run by
CSL Behring
See details and how to joinNCT06003387 · EU 2023-509590-23-00
Phase 4Enrolling by invitation
A Long-Term Follow-Up Study in Severe Hemophilia A Subjects Who Received BMN 270 in a Prior BioMarin Clinical Trial (270-401)
Where
Adelaide, Herston, Melbourne, Murdoch, Sydney
Age
18 years and over
People
172 worldwide
Run by
BioMarin Pharmaceutical
See details and how to joinNCT05768386 · EU 2023-507749-27-00