Haemophilia trials in Brazil

In Brazil 11 Also abroad 128

11 trials · From ClinicalTrials.gov, checked 10 November 2026. Ask the study team whether a trial fits you.

Phase 3Taking people
A Clinical Study to Evaluate the Effects of NXT007 Compared to Emicizumab Prophylaxis in People With Hemophilia A
Where
Ribeirão Preto, São Paulo
Age
12 years and over
People
360 worldwide
Run by
Hoffmann-La Roche
See details and how to joinNCT07416604 · EU 2025-522435-33-00
Phase 3Taking people
A Research Study Investigating Denecimig (Mim8) in Adults With Acquired Haemophilia A
Where
Distrito de Barão Geraldo - Campinas, Ribeirão Preto, Rio de Janeiro, São Paulo
Age
18 years and over
People
84 worldwide
Run by
Novo Nordisk A/S
See details and how to joinNCT07830732 · EU 2026-525529-19-00
Phase 3Taking people
A Study to Investigate the Efficacy and Safety of Fitusiran Prophylaxis in Male Participants Aged 1 to Less Than 12 Years With Hemophilia A or B
Where
Campinas, Ribeirão Preto, São Paulo
Age
1 year to 11 years
People
85 worldwide
Run by
Sanofi
See details and how to joinNCT07285460 · EU 2025-521858-42-00
Phase 3Taking people
Open-Label Extension Study of Marstacimab in Hemophilia Participants With or Without Inhibitors
Where
Vitória
Age
1 year to 74 years
People
245 worldwide
Run by
Pfizer
See details and how to joinNCT05145127 · EU 2022-500470-33-00
No phaseTaking people
An Observational Study to Learn More About How Well Damoctocog Alfa Pegol Works in Previously Treated Children With Hemophilia A
Where
Many Locations
Age
7 years to 12 years
People
40 worldwide
Run by
Bayer
See details and how to joinNCT07088458
Phase 3Taking people
A Clinical Study to Evaluate the Effects of NXT007 Compared to Factor VIII Prophylaxis in Participants With Hemophilia A
Where
Campinas, Ribeirão Preto
Age
12 years and over
People
138 worldwide
Run by
Hoffmann-La Roche
See details and how to joinNCT07416526 · EU 2025-522434-32-00
Phase 1/2Taking people
A Study to Investigate the Safety and Effectiveness of a Coagulation Factor IX Gene Insertion Therapy (REGV131-LNP1265) in Pediatric, Adolescent and Adult Participants With Hemophilia B
Where
Campinas, Rio de Janeiro, Vitória
Age
2 years and over
People
130 worldwide
Run by
Regeneron Pharmaceuticals
See details and how to joinNCT06379789 · EU 2023-507260-40-00
Phase 3Taking people
A Clinical Trial of Study Medicine (Marstacimab) in Pediatric Patients With Hemophilia A or Hemophilia B
Where
Maruípe
Age
1 year to 17 years
People
100 worldwide
Run by
Pfizer
See details and how to joinNCT05611801 · EU 2022-500495-65-00
Phase 3Taking people
Efficacy and Safety of CSL222 (Etranacogene Dezaparvovec) Gene Therapy in Adults With Hemophilia B With Pretreatment Adeno-associated Virus Serotype 5 (AAV5) Neutralizing Antibodies (Nabs)
Where
São Paulo
Age
18 years and over
People
35 worldwide
Run by
CSL Behring
See details and how to joinNCT06003387 · EU 2023-509590-23-00
Phase 4Enrolling by invitation
A Long-Term Follow-Up Study in Severe Hemophilia A Subjects Who Received BMN 270 in a Prior BioMarin Clinical Trial (270-401)
Where
Campinas, Rio de Janeiro, São Paulo, Vitória
Age
18 years and over
People
172 worldwide
Run by
BioMarin Pharmaceutical
See details and how to joinNCT05768386 · EU 2023-507749-27-00
No phaseTaking people
Embolization in Hereditary Coagulopathies
Where
São Paulo
People
30
Run by
University of Sao Paulo General Hospital
See details and how to joinNCT05629130